Correcting SMN2 splicing with tailed antisense oligoribonucleotides: a promising therapeutic strategy for spinal muscular atrophy

被引：0
|
作者：
Zhou, H. [1 ]
Owen, N. [2 ]
Eperon, I. C. [2 ]
Muntoni, F. [1 ]
机构：
[1] UCL, Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
[2] Univ Leicester, Dept Biochem, Leicester LE1 7RH, Leics, England
来源：
NEUROMUSCULAR DISORDERS | 2009年 / 19卷 / 8-9期
关键词：
D O I：
10.1016/j.nmd.2009.06.112
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：578 / 578
页数：1
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