Antisense-Mediated Exon Skipping for Duchenne Muscular Dystrophy

被引：0
|
作者：
Aartsma-Rus, Annemieke [1 ]
Heemskerk, Hans [1 ]
de Winter, Christa [1 ]
van Putten, Maaike [1 ]
Janson, Anneke [2 ]
Verschuuren, Jan [3 ]
den Dunnen, Johan [1 ]
van Deutekom, Judith [2 ]
van Ommen, Gert-Jan [1 ]
机构：
[1] Leiden Univ, Dept Human Genet, Med Ctr, NL-2300 RA Leiden, Netherlands
[2] Prosensa Therapeut BV, Leiden, Netherlands
[3] Leiden Univ, Med Ctr, Dept Neurol, Leiden, Netherlands
来源：
HUMAN GENE THERAPY | 2009年 / 20卷 / 06期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：660 / 661
页数：2
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