Achievement of Normal Circulating Factor VIII Activity Following Bmn 270 AAV5-FVIII Gene Transfer: Interim, Long-Term Efficacy and Safety Results from a Phase 1/2 Study in Patients with Severe Hemophilia a

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作者：
Pasi, K. John
Rangarajan, Savita
Kim, Benjamin
Lester, Will
Perry, David
Madan, Bella
Tavakkoli, Fatemeh
Yang, Ke
Pierce, Glenn F.
Wong, Wing Yen
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BLOOD | 2017年 / 130卷
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R5 [内科学];
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1002 ; 100201 ;
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603
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页数：1
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