Spk-8011: Preliminary Results from a Phase 1/2 Dose Escalation Trial of an Investigational AAV-Mediated Gene Therapy for Hemophilia a

被引：0
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作者：
George, Lindsey A.
Ragni, Margaret V.
Samelson-Jones, Ben J.
Cuker, Adam
Runoski, Alexa R.
Cole, Grace
Wright, Fraser
Chen, Yifeng
Hui, Daniel J.
Wachtel, Katie
Takefman, Daniel
Couto, Linda B.
Reape, Kathleen Z.
Carr, Marcus E.
Anguela, Xavier M.
High, Katherine A.
机构：
来源：
BLOOD | 2017年 / 130卷
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R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
604
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页数：2
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