Site-Specific Genome Editing in Human Long-Term Repopulating Hematopoietic Stem Cells for Correction of SCID-X1

被引：0

作者：

Genovese, Pietro ^{[1
]}

Schiroli, Giulia ^{[1
,2
]}

Escobar, Giulia ^{[1
,2
]}

Di Tomaso, Tiziano ^{[1
]}

Firrito, Claudia ^{[1
]}

Moi, Davide ^{[1
]}

Benedicenti, Fabrizio ^{[1
]}

Calabria, Andrea ^{[1
]}

Mazzieri, Roberta ^{[1
]}

Gregory, Philip D. ^{[3
]}

Holmes, Michael C. ^{[3
]}

van der Burg, Mirjam ^{[4
]}

Montini, Eugenio ^{[1
]}

Gentner, Bernhard ^{[1
]}

Lombardo, Angelo ^{[1
,2
]}

Naldini, Luigi ^{[1
,2
]}

机构：

[1] San Raffaele TIGET, Milan, Italy

[2] Univ Vita Salute San Raffaele, Milan, Italy

[3] Sangamo BioSci, Richmond, CA USA

[4] Erasmus MC, Rotterdam, Netherlands

来源：

MOLECULAR THERAPY | 2014年 / 22卷

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

754

引用

页码：S291 / S291

页数：1

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