Site-Specific Genome Editing in Human Long-Term Repopulating Hematopoietic Stem Cells for Correction of SCID-X1

被引：0
|
作者：
Genovese, Pietro [1 ]
Schiroli, Giulia [1 ,2 ]
Escobar, Giulia [1 ,2 ]
Di Tomaso, Tiziano [1 ]
Firrito, Claudia [1 ]
Moi, Davide [1 ]
Benedicenti, Fabrizio [1 ]
Calabria, Andrea [1 ]
Mazzieri, Roberta [1 ]
Gregory, Philip D. [3 ]
Holmes, Michael C. [3 ]
van der Burg, Mirjam [4 ]
Montini, Eugenio [1 ]
Gentner, Bernhard [1 ]
Lombardo, Angelo [1 ,2 ]
Naldini, Luigi [1 ,2 ]
机构：
[1] San Raffaele TIGET, Milan, Italy
[2] Univ Vita Salute San Raffaele, Milan, Italy
[3] Sangamo BioSci, Richmond, CA USA
[4] Erasmus MC, Rotterdam, Netherlands
来源：
MOLECULAR THERAPY | 2014年 / 22卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
754
引用
收藏
页码：S291 / S291
页数：1
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