[1] Univ Iowa, Program Gene Therapy, Iowa City, IA USA
[2] Univ Iowa, Dept Internal Med, Iowa City, IA 52242 USA
[3] Univ Iowa, Dept Neurol, Iowa City, IA 52242 USA
[4] Univ Iowa, Dept Physiol & Biophys, Iowa City, IA 52242 USA
[5] NHLBI, NIH, Bethesda, MD 20892 USA
[6] Baylor Coll Med, Howard Hughes Med Inst, Houston, TX 77030 USA
[7] Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
[8] Baylor Coll Med, Dept Pediat, Houston, TX 77030 USA
[9] Baylor Coll Med, Program Dev Biol, Houston, TX 77030 USA
[10] Univ Minnesota, Inst Human Genet, Minneapolis, MN 55455 USA