Eliglustat in patients with Gaucher disease previously treated with enzyme replacement therapy: Real-life experience from Israel

被引：0

作者：

Istaiti, Majdolen ^{[1
]}

Ruhrman-Shahar, Noa ^{[2
]}

Cohen, Ian J. ^{[2
]}

Hershkovitz, Tova ^{[3
]}

Becker-Cohen, Michal ^{[1
]}

Dinur, Tama ^{[1
]}

Revel-Vilk, Shoshana ^{[4
]}

Zimran, Ari ^{[1
]}

机构：

[1] Shaare Zedek Med Ctr, Gaucher Unit, Jerusalem, Israel

[2] Beilinson Med Ctr, Raphael Recanati Genet Inst, Rabin Med Ctr, Gaucher Clin, Petah Tiqwa, Israel

[3] Rambam Hlth Care Campus, Genet Inst, Haifa, Israel

[4] Shaare Zedek Med Ctr, Pediat Hematol Oncol Unit, Gaucher Unit, Jerusalem, Israel

来源：

MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2021.11.151

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

136

引用

页码：S61 / S61

页数：1

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