Eliglustat in patients with Gaucher disease previously treated with enzyme replacement therapy: Real-life experience from Israel

被引：0
|
作者：
Istaiti, Majdolen [1 ]
Ruhrman-Shahar, Noa [2 ]
Cohen, Ian J. [2 ]
Hershkovitz, Tova [3 ]
Becker-Cohen, Michal [1 ]
Dinur, Tama [1 ]
Revel-Vilk, Shoshana [4 ]
Zimran, Ari [1 ]
机构：
[1] Shaare Zedek Med Ctr, Gaucher Unit, Jerusalem, Israel
[2] Beilinson Med Ctr, Raphael Recanati Genet Inst, Rabin Med Ctr, Gaucher Clin, Petah Tiqwa, Israel
[3] Rambam Hlth Care Campus, Genet Inst, Haifa, Israel
[4] Shaare Zedek Med Ctr, Pediat Hematol Oncol Unit, Gaucher Unit, Jerusalem, Israel
来源：
MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2021.11.151
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
136
引用
收藏
页码：S61 / S61
页数：1
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