RAPID CORRECTION OF ORNITHINE TRANSCARBAMYLASE DEFICIENCY (OTCD) IN AN OTCD MOUSE MODEL USING A SELF-COMPLEMENTARY AAV2/8 VECTOR

被引：0
|
作者：
Jones, D. J. [1 ]
Wang, H. [2 ]
Bell, P. [2 ]
Avilan-Dorante, A. [2 ]
Gao, G. [3 ]
Batshaw, M. L. [4 ]
Wilson, J. M. [2 ]
Wang, L. [2 ]
Morizono, H. [1 ]
机构：
[1] Childrens Natl Med Ctr, Ctr Genet Med, Washington, DC 20010 USA
[2] Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA 19104 USA
[3] Univ Massachusetts, Sch Med, Gene Therapy Ctr, Worcester, MA USA
[4] Childrens Natl Med Ctr, Childrens Res Inst, Washington, DC 20010 USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2009年 / 98卷 / 1-2期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
728
引用
收藏
页码：147 / 147
页数：1
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