[1] Univ Florida, Coll Med, Dept Biochem & Mol Biol, Ctr Struct Biol,McKnight Brain Inst, Gainesville, FL 32610 USA
[2] Univ N Carolina, Dept Genet, Chapel Hill, NC USA
[3] Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC USA
[4] Univ Florida, Dept Pediat, Gainesville, FL USA
[5] Univ Florida, Coll Med, Div Cell & Mol Therapy, Powell Gene Therapy Ctr, Gainesville, FL USA