The Longer-term Efficacy and Safety of Evinacumab in Patients With Homozygous Familial Hypercholesterolemia

被引:0
|
作者
Raal, Frederick J.
Rosenson, Robert S.
Reeskamp, Laurens F.
Hovingh, G. Kees
Kastelein, John J.
Rubba, Paolo
Ali, Shazia
Banerjee, Poulabi
Chan, Kuo-Chen
Khilla, Nagwa
Pordy, Robert
Zhang, Yi
Gaudet, Daniel
机构
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
A14407
引用
收藏
页数:2
相关论文
共 50 条
  • [31] Lessons learned from the evinacumab trials in the treatment of homozygous familial hypercholesterolemia
    Khoury, Etienne
    Croteau, Laurent
    Lauziere, Alex
    Gaudet, Daniel
    FUTURE CARDIOLOGY, 2022, 18 (06) : 507 - 518
  • [32] Dramatic response to Evinacumab in a North Indian girl with homozygous familial hypercholesterolemia
    Arora, Sonali
    Banerjee, Sayan
    George, Arun
    Bala, Anju
    Thingnam, Shyam Kumar Singh
    Rohit, Manoj Kumar
    Dayal, Devi
    JOURNAL OF PEDIATRIC ENDOCRINOLOGY & METABOLISM, 2025, 38 (03): : 305 - 309
  • [33] Evinacumab for Homozygous Familial Hypercholesterolemia: The Italian Cohort of the ELIPSE HoFH Study
    Gabriella Iannuzzo
    Ilenia Calcaterra
    Marco Gentile
    Claudia Stanzione
    Francesca De Ruberto
    Maria Donata Di Taranto
    Giuliana Fortunato
    Matteo Di Minno
    Advances in Therapy, 2025, 42 (5) : 2465 - 2479
  • [34] Population pharmacokinetics and exposure-response modeling for evinacumab in homozygous familial hypercholesterolemia
    Pu, Xia
    Sale, Mark
    Yang, Feng
    Zhang, Yi
    Davis, John D.
    Al-Huniti, Nidal
    CPT-PHARMACOMETRICS & SYSTEMS PHARMACOLOGY, 2021, 10 (11): : 1412 - 1421
  • [35] Long-Term Efficacy and Safety of the Microsomal Triglyceride Transfer Protein Inhibitor Lomitapide in Patients With Homozygous Familial Hypercholesterolemia
    Blom, Dirk J.
    Averna, Maurizio R.
    Meagher, Emma A.
    Theron, Hendrik du Toit
    Sirtori, Cesare R.
    Hegele, Robert A.
    Shah, Prediman K.
    Gaudet, Daniel
    Stefanutti, Claudia
    Vigna, Giovanni B.
    Larrey, Dominique
    Bloedon, LeAnne T.
    Foulds, Pamela
    Rader, Daniel J.
    Cuchel, Marina
    CIRCULATION, 2017, 136 (03) : 332 - 335
  • [36] Efficacy of evinacumab in homozygous familial hypercholesterolemia patients with null or non-null LDL-receptor mutations and on various background therapies
    Hovingh, G. K.
    Gipe, D. A.
    Ahmad, Z.
    Cuchel, M.
    Shah, P.
    Chyu, K. Y.
    Pordy, R.
    Sasiela, W. J.
    Chan, K. C.
    Khoury, E.
    Gaudet, D.
    EUROPEAN HEART JOURNAL, 2017, 38 : 1252 - 1252
  • [37] EVINACUMAB MARKEDLY REDUCES LOW-DENSITY LIPOPROTEIN CHOLESTEROL IN ADOLESCENT PATIENTS WITH HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA
    Reeskamp, L. F.
    Greber-Platzer, S.
    Saheb, S.
    Stefanutti, C.
    Stroes, E. S. G.
    Ali, S.
    Banerjee, P.
    Pordy, R.
    Zhao, J.
    Raal, F. J.
    ATHEROSCLEROSIS, 2021, 331 : E49 - E50
  • [38] Real-World Effectiveness and Safety of Evinacumab in Pediatric and Adult Patients With Homozygous Familial Hypercholesterolemia: A Multi-Site US Perspective
    Wilkinson, Michael J.
    Bijlani, Priyesha
    Davidson, Michael H.
    Duell, P. B.
    Horan, Mary
    Malloy, Mary J.
    Newfield, Ron
    Pradeep, Pallavi
    Sam, Colleen
    Shah, Prediman K.
    Stock, Eveline O.
    Warden, Bruce
    Ito, Matthew K.
    CIRCULATION, 2023, 148
  • [39] EVINACUMAB MARKEDLY REDUCES LOW-DENSITY LIPOPROTEIN CHOLESTEROL IN ADOLESCENT PATIENTS WITH HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA
    Reeskamp, Rens
    Greber-Platzer, Susanne
    Saheb, Samir
    Stefanutti, Claudia
    Stroes, Erik S. G.
    Ali, Shazia
    Pordy, Robert
    Zhao, Jian
    Raal, Frederick J.
    JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, 2021, 77 (18) : 121 - 121
  • [40] Transscleral diode laser cyclophotocoagulation: Longer-term efficacy and safety
    Riaz, Y
    George, SM
    Wilson, C
    Seeberan, RA
    Franks, WA
    Barton, K
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2005, 46