Toxicity & Biodistribution Study Demonstrates Safety of AAV-Mediated Human Beta-Sarcoglycan Gene Therapy

被引：0
|
作者：
Pozsgai, Eric [1 ]
Griffin, Danielle [1 ]
Heller, Kristin [1 ]
Mendell, Jerry [1 ]
Rodino-Klapac, Louise [1 ]
机构：
[1] Nationwide Childrens Hosp, Columbus, OH USA
来源：
MOLECULAR THERAPY | 2017年 / 25卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
40
引用
收藏
页码：19 / 20
页数：2
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