[1] BioMarin Pharmaceut Inc, Novato, CA 94949 USA
[2] Harbor UCLA Med Ctr, Dept Pediat, Torrance, CA 90502 USA
[3] Harbor UCLA Med Ctr, Dept Ophthalmol, Torrance, CA 90502 USA
[4] Harbor UCLA Med Ctr, Dept Med, Torrance, CA 90502 USA
[5] Harbor UCLA Med Ctr, Dept Radiol, Torrance, CA 90502 USA
[6] Harbor UCLA Med Ctr, Dept Phys Therapy, Torrance, CA 90502 USA
[7] Genzyme Corp, Clin Res, Cambridge, MA 02142 USA