[1] UCL Great Ormond St Inst Child Hlth, Dubowitz Neuromuscular Ctr, 30 Guilford St, London WC1N 1EH, England
[2] UCL Great Ormond St Inst Child Hlth, Populat Policy & Practice Res & Teaching Dept, London, England
[3] UCL Great Ormond St Inst Child Hlth, NIHR Great Ormond St Hosp Biomed Res Ctr, London, England
[4] Natl Ctr Neurol & Psychiat NCNP, Dept Mol Therapy, Natl Inst Neurosci, Kodaira, Japan
[5] UCL, Dept Cell & Dev Biol, London, England
[6] Queen Mary Univ London, Ctr Genom & Child Hlth, Blizard Inst, Barts & London Sch Med & Dent, London, England
[7] Francis Crick Inst, London, England