Comparison of ZFNs versus CRISPR specific nucleases for genome edition of the Wiskott-Aldrich Syndrome locus

被引：0

作者：

Sanchez-Hernandez, S. ^{[1
]}

Gutierrez-Guerrero, A. ^{[1
]}

Galvani, G. ^{[1
]}

Pinedo-Gomez, J. ^{[1
]}

Cobo, M. ^{[1
]}

Martin, R. ^{[1
]}

Aguilar-Gonzalez, A. ^{[1
]}

Gregory, P. D. ^{[2
]}

Holmes, M. C. ^{[2
]}

Benabdellah, K. ^{[1
]}

Martin, F. ^{[1
]}

机构：

[1] Pfizer Univ Granada Junta Andalucia, GENyO Ctr Genom & Invest Oncol, Granada, Spain

[2] Sangamo BioSci Inc, Richmond, CA USA

来源：

HUMAN GENE THERAPY | 2017年 / 28卷 / 12期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P150

引用

页码：A59 / A59

页数：1

共 44 条

[21] Comparison of Gene Editing Strategies for Gene Correction of Wiskott-Aldrich Syndrome in Mouse Embryonic Stem Cells
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[22] THE WISKOTT-ALDRICH SYNDROME - REFINEMENT OF THE LOCALIZATION ON XP AND IDENTIFICATION OF ANOTHER CLOSELY LINKED MARKER LOCUS, OATL1
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HUMAN GENETICS, 1992, 88 (04) : 453 - 456
[23] Leucoderma and leucotrichia in association with chronic cutaneous graft-versus-host disease in a child with Wiskott-Aldrich syndrome
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[24] Use of zinc-finger nucleases to knock out the WAS gene in K562 cells: a human cellular model for Wiskott-Aldrich syndrome
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[25] GRAFT VERSUS HOST REACTION IN WISKOTT-ALDRICH SYNDROME - ANTEMORTEM DIAGNOSIS OF HUMAN GVH IN AN IMMUNOLOGIC DEFICIENCY DISEASE
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[26] Hematopoietic-specific lentiviral vectors circumvent cellular toxicity due to ectopic expression of Wiskott-Aldrich syndrome protein
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Frecha, Cecilia
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[27] Defective T-cell education by dendritic cells contributes to impaired antigen specific immunity in Wiskott-Aldrich syndrome
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CLINICAL AND EXPERIMENTAL IMMUNOLOGY, 2008, 154 : 157 - 158
[28] THE UDP-GALACTOSE TRANSLOCATOR GENE IS MAPPED TO BAND-XP11.23-P11.22 CONTAINING THE WISKOTT-ALDRICH SYNDROME LOCUS
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YAMAUCHI, M
TAKAHASHI, E
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AOKI, K
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SOMATIC CELL AND MOLECULAR GENETICS, 1993, 19 (06) : 571 - 575
[29] Scarless correction of Wiskott Aldrich Syndrome patient-specific iPSCs using CRISPR/Cas9 and piggyBac
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[30] Multi-lineage analysis of X-inactivation in female carriers of genetic alterations in the Wiskott-Aldrich syndrome protein (WASP) gene locus
Moratto, D.
Forino, C.
Notarangelo, L. D.
Vielmi, V.
Mazza, C.
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Zecca, M.
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Porta, F.
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CLINICAL AND EXPERIMENTAL IMMUNOLOGY, 2008, 154 : 68 - 69

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