Pulmonary Function in Advanced Duchenne Muscular Dystrophy: Eteplirsen-Treated Patients versus Multiple Natural History Cohorts

被引:0
|
作者
Gordish-Dressman, Heather [1 ]
Henricson, Erik [2 ]
Han, Lixin [3 ]
Dugar, Ashish [3 ]
McDonald, Craig M. [2 ]
机构
[1] George Washington Univ, Sch Med & Hlth Sci, Washington, DC 20052 USA
[2] Univ Calif Davis, Davis, CA 95616 USA
[3] Sarepta Therapeut Inc, Cambridge, MA USA
[4] CINRG DNHS, Pittsburgh, PA USA
关键词
D O I
暂无
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
M279
引用
收藏
页码:S219 / S220
页数:2
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