Improvement in Health-Related Quality of Life Following Treatment with Betibeglogene Autotemcel in Patients with Transfusion-Dependent ß-Thalassemia Enrolled in Phase 3 Studies

被引：3
|
作者：
Kwiatkowski, Janet L. [1 ,2 ]
Locatelli, Franco [3 ]
Walters, Mark C. [4 ]
Porter, John B. [5 ]
Hongeng, Suradej [6 ]
Yannaki, Evangelia [7 ]
Kulozik, Andreas E. [8 ,9 ]
Sauer, Martin G. [10 ]
Thrasher, Adrian J. [11 ]
Thuret, Isabelle [12 ]
Lal, Ashutosh [4 ]
Guo, Ruiting [13 ]
Colvin, Richard A. [13 ]
Gruppioni, Katiana [13 ]
Thompson, Alexis A. [14 ,15 ]
机构：
[1] Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA USA
[2] Childrens Hosp Philadephia, Div Hematol, Philadelphia, PA USA
[3] IRCCS Bambino Gesu Childrens Hosp, Dept Pediat Hematol Oncol, Cell & Gene Therapy, Rome, Italy
[4] UCSF Benioff Childrens Hosp Oakland, Div Hematol, Oakland, CA USA
[5] Univ Coll London Hosp, Dept Haematol, London, England
[6] Mahidol Univ, Ramathibodi Hosp, Bangkok, Thailand
[7] G Papanikolaou Hosp, Hematol HCT Unit, Gene & Cell Therapy Ctr, Thessaloniki, Greece
[8] Heidelberg Univ, Mol Med Partnership Unit MMPU, European Mol Biol Lab EMBL, Heidelberg, Germany
[9] Heidelberg Univ, Dept Pediat Oncol Hematol & Immunol, Heidelberg, Germany
[10] Hannover Med Sch, Dept Hematol & Oncol, Hannover, Germany
[11] UCL Great Ormond St Inst Child Hlth, London, England
[12] Hop La Timone, Pediat Hematol, Marseille, France
[13] Bluebird Bio Inc, Cambridge, MA USA
[14] Ann Robert H Lurie Childrens Hosp Chicago, Hematol Sect, Chicago, IL USA
[15] Northwestern Univ, Dept Pediat Hematol Oncol & Stem Cell Transplant, Feinberg Sch Med, Chicago, IL USA
来源：
BLOOD | 2021年 / 138卷
关键词：
D O I：
10.1182/blood-2021-150392
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
3085
引用
收藏
页数：6
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