Antisense Oligonucleotide Therapy for Lafora Disease

被引：0
|
作者：
Ahonen, Saija [1 ]
Grossman, Tamar [2 ]
Turnbull, Julie [1 ]
Kordasiewicz, Holly [2 ]
Katz, Melanie [2 ]
McCaleb, Michael [2 ]
Wang, Peixiang [1 ]
Zhao, Xiaochu [1 ]
Minassian, Berge [3 ]
机构：
[1] Hosp Sick Children, Toronto, ON, Canada
[2] Ionis Pharmaceut, San Diego, CA USA
[3] Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA
来源：
NEUROLOGY | 2018年 / 90卷
关键词：
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
S53.005
引用
收藏
页数：2
相关论文
共 50 条
  • [41] Alzheimer disease: Antisense oligonucleotide reverses tau pathology
    Crunkhorn S.
    Nature Reviews Drug Discovery, 2017, 16 (3) : 166 - 166
  • [42] Antisense Oligonucleotide Reverses Leukodystrophy in Canavan Disease Mice
    Hull, Vanessa
    Wang, Yan
    Burns, Travis
    Zhang, Sheng
    Sternbach, Sarah
    McDonough, Jennifer
    Guo, Fuzheng
    Pleasure, David
    ANNALS OF NEUROLOGY, 2020, 87 (03) : 480 - 485
  • [43] Reviewing antisense oligonucleotide therapy, part 1 - Action and design
    Das, SK
    Miller, KJ
    BIOPHARM-THE APPLIED TECHNOLOGIES OF BIOPHARMACEUTICAL DEVELOPMENT, 1999, 12 (10): : 42 - +
  • [44] Fetal antisense oligonucleotide therapy for congenital deafness and vestibular dysfunction
    Wang, Lingyan
    Kempton, J. Beth
    Jiang, Han
    Jodelka, Francine M.
    Brigande, Alev M.
    Dumont, Rachel A.
    Rigo, Frank
    Lentz, Jennifer J.
    Hastings, Michelle L.
    Brigande, John, V
    NUCLEIC ACIDS RESEARCH, 2020, 48 (09) : 5065 - 5080
  • [45] Recent Advances in Antisense Oligonucleotide Therapy in Genetic Neuromuscular Diseases
    Verma, Ashok
    ANNALS OF INDIAN ACADEMY OF NEUROLOGY, 2018, 21 (01) : 3 - 8
  • [46] Reviewing antisense oligonucleotide therapy: part 2, delivery issues
    Das, SK
    Miller, KJ
    BIOPHARM-THE APPLIED TECHNOLOGIES OF BIOPHARMACEUTICAL DEVELOPMENT, 1999, 12 (11): : 44 - +
  • [47] Carbohydrate modifications in antisense oligonucleotide therapy: New kids on the block
    Manoharan, M
    Kawasaki, AM
    Prakash, TP
    Fraser, AS
    Prhavc, M
    Inamati, GB
    Casper, MD
    Cook, PD
    NUCLEOSIDES NUCLEOTIDES & NUCLEIC ACIDS, 1999, 18 (6-7): : 1737 - 1746
  • [48] Basics of antisense oligonucleotide therapy and current therapeutical strategies in urology
    Kausch, I
    Böhle, A
    AKTUELLE UROLOGIE, 2003, 34 (07) : 458 - 468
  • [49] Antisense Oligonucleotide Therapy against Spinal Muscular Dystrophy approved
    Pacher-Zavisin, Margit C.
    BIOENGINEERED, 2017, 8 (02) : 114 - 114
  • [50] Antisense Oligonucleotide-Based Therapy in Human Erythropoietic Protoporphyria
    Oustric, Vincent
    Manceau, Hana
    Ducamp, Sarah
    Soaid, Rima
    Karim, Zoubida
    Schmitt, Caroline
    Mirmiran, Arienne
    Peoc'h, Katell
    Grandchamp, Bernard
    Beaumont, Carole
    Lyoumi, Said
    Moreau-Gaudry, Francois
    Guyonnet-Duperat, Veronique
    de Verneuil, Hubert
    Marie, Joelle
    Puy, Herve
    Deybach, Jean-Charles
    Gouya, Laurent
    AMERICAN JOURNAL OF HUMAN GENETICS, 2014, 94 (04) : 611 - 617
12345