Gene therapy targets sickle-cell disease

被引:0
|
作者
Nowogrodzki, Anna
机构
关键词
Diseases; Gene therapy; Medical research; Stem cells;
D O I
10.1038/d41586-018-07646-w
中图分类号
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号
07 ; 0710 ; 09 ;
摘要
The research is promising, but a true cure for this painful condition could be years away.
引用
收藏
页码:S12 / S13
页数:1
相关论文
共 50 条
  • [21] An in vitro and in vivo comparison of lentiviral vectors for gene therapy of sickle-cell disease
    Urbinati, F.
    Poletti, V.
    Fernandez, B. C.
    Martin, S.
    Hollis, R. P.
    Koziol, C.
    Kaufman, M. L.
    Brown, D.
    Miccio, A.
    Antoniou, M.
    Mavilio, F.
    Kohn, D. B.
    HUMAN GENE THERAPY, 2016, 27 (11) : A113 - A114
  • [22] Africa must participate in finding a gene therapy cure for sickle-cell disease
    Moshi, Grace
    Sheehan, Vivien A.
    Makani, Julie
    NATURE MEDICINE, 2022, 28 (12) : 2451 - 2452
  • [23] RECOMBINANT HUMAN HEMOGLOBINS DESIGNED FOR GENE-THERAPY OF SICKLE-CELL DISEASE
    MCCUNE, SL
    REILLY, MP
    CHOMO, MJ
    ASAKURA, T
    TOWNES, TM
    PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1994, 91 (21) : 9852 - 9856
  • [24] Africa must participate in finding a gene therapy cure for sickle-cell disease
    Grace Moshi
    Vivien A. Sheehan
    Julie Makani
    Nature Medicine, 2022, 28 : 2451 - 2452
  • [25] SICKLE-CELL DISEASE
    BROZOVIC, M
    PRACTITIONER, 1982, 226 (1368) : 1009 - 1009
  • [26] SICKLE-CELL DISEASE
    PEGELOW, C
    POWARS, D
    OVERTURF, GD
    AMERICAN JOURNAL OF DISEASES OF CHILDREN, 1979, 133 (04): : 448 - 448
  • [27] SICKLE-CELL DISEASE
    MAKLER, MT
    BRITISH JOURNAL OF HAEMATOLOGY, 1981, 48 (02) : 355 - 356
  • [28] Sickle-cell disease
    Thomas, Michael John Glyn
    TRAVEL MEDICINE AND INFECTIOUS DISEASE, 2010, 8 (01) : 62 - 63
  • [29] SICKLE-CELL DISEASE
    EDELSTEIN, SJ
    NATURE, 1976, 260 (5547) : 98 - 100
  • [30] Sickle-cell disease
    Herb Brody
    Nature, 2021, 596 : S1 - S1