Significant disease burden in paroxysmal nocturnal haemoglobinuria (PNH) patients with lower levels of haemolysis, mild anaemia and minimal transfusion: clinical improvement with eculizumab therapy

被引:0
|
作者
Hill, A. [1 ]
Bessler, M. [2 ]
Schrezenmeier, H. [3 ]
Maciejewski, J. P. [4 ]
Rollins, S. A. [5 ]
Young, N. S. [6 ]
Luzzatto, L. [7 ]
机构
[1] Bradford Royal Infirm, Dept Haematol, Bradford, W Yorkshire, England
[2] Washington Univ, Sch Med, St Louis, MD USA
[3] Inst Clin Transfus Med & Immunogenet, Ulm, Germany
[4] Cleveland Clin, Cleveland, OH 44106 USA
[5] Alex Pharmaceut, Cheshire, CT USA
[6] NHLBI, Bethesda, MD 20892 USA
[7] Ist Toscano Tumori, Florence, Italy
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
180
引用
收藏
页码:66 / 67
页数:2
相关论文
共 14 条
  • [11] Design and development of a disease-specific quality of life tool for patients with aplastic anaemia and/or paroxysmal nocturnal haemoglobinuria (QLQ-AA/PNH)—a report on phase III
    Cathrin Niedeggen
    Susanne Singer
    Martha Groth
    Andrea Petermann-Meyer
    Alexander Röth
    Hubert Schrezenmeier
    Britta Höchsmann
    Tim H. Brümmendorf
    Jens Panse
    Annals of Hematology, 2019, 98 : 1547 - 1559
  • [12] Design and development of a disease-specific quality of life tool for patients with aplastic anaemia and/or paroxysmal nocturnal haemoglobinuria (QLQ-AA/PNH)a report on phase III
    Niedeggen, Cathrin
    Singer, Susanne
    Groth, Martha
    Petermann-Meyer, Andrea
    Roeth, Alexander
    Schrezenmeier, Hubert
    Hoechsmann, Britta
    Bruemmendorf, Tim H.
    Panse, Jens
    ANNALS OF HEMATOLOGY, 2019, 98 (07) : 1547 - 1559
  • [13] Predictors for improvement in patient-reported outcomes: post hoc analysis of a phase 3 randomised, open-label study of eculizumab and ravulizumab in complement inhibitor-naive patients with paroxysmal nocturnal haemoglobinuria (PNH)
    Schrezenmeier, Hubert
    Kulasekararaj, Austin
    Mitchell, Lindsay
    de latour, Regis Peffault
    Devos, Timothy
    Okamoto, Shinichiro
    Wells, Richard
    Popoff, Evan
    Cheung, Antoinette
    Johnston, Karissa
    Wang, Jimmy
    Gustovic, Philippe
    Wang, Alice
    Tomazos, Ioannis
    Patel, Yogesh
    Lee, Jong Wook
    BRITISH JOURNAL OF HAEMATOLOGY, 2022, 197 : 136 - 137
  • [14] SIGNIFICANT DISEASE BURDEN EVALUATED BY FACIT-FATIGUE AND EORTC QLQ-C30 IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA FROM A KOREAN PROSPECTIVE PNH REGISTRY
    Lee, J. W.
    Jang, J. H.
    Kim, J. S.
    Lee, J. H.
    Park, J. S.
    Chung, J. S.
    Lee, J. H.
    Kim, J. A.
    Jo, D. Y.
    Park, Y.
    HAEMATOLOGICA, 2014, 99 : 218 - 219