Significant disease burden in paroxysmal nocturnal haemoglobinuria (PNH) patients with lower levels of haemolysis, mild anaemia and minimal transfusion: clinical improvement with eculizumab therapy

被引:0
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作者
Hill, A. [1 ]
Bessler, M. [2 ]
Schrezenmeier, H. [3 ]
Maciejewski, J. P. [4 ]
Rollins, S. A. [5 ]
Young, N. S. [6 ]
Luzzatto, L. [7 ]
机构
[1] Bradford Royal Infirm, Dept Haematol, Bradford, W Yorkshire, England
[2] Washington Univ, Sch Med, St Louis, MD USA
[3] Inst Clin Transfus Med & Immunogenet, Ulm, Germany
[4] Cleveland Clin, Cleveland, OH 44106 USA
[5] Alex Pharmaceut, Cheshire, CT USA
[6] NHLBI, Bethesda, MD 20892 USA
[7] Ist Toscano Tumori, Florence, Italy
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R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
180
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页码:66 / 67
页数:2
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