Enhanced factor VIII gene therapy for hemophilia a dogs with a novel Furin-evading factor VIII variant

被引：0

作者：

Siner, J., I ^{[1
]}

Samelson-Jones, B. ^{[1
]}

Crudele, J. M. ^{[2
]}

Zhou, S. ^{[3
]}

Merricks, E. ^{[4
]}

Nichols, T. ^{[4
]}

Camire, R. M. ^{[1
]}

Arruda, V. R. ^{[1
]}

机构：

[1] Childrens Hosp Philadelphia, Div Hematol, Pediat, Philadelphia, PA 19104 USA

[2] Univ Penn, Philadelphia, PA 19104 USA

[3] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA

[4] Univ N Carolina, Pathol & Lab Med, Chapel Hill, NC USA

来源：

JOURNAL OF THROMBOSIS AND HAEMOSTASIS | 2015年 / 13卷

关键词：

D O I：

暂无

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

AS120

引用

页码：43 / 43

页数：1

共 50 条

[31] Enhanced Gene Expression of Factor VIII by Ultrasound-Mediated Gene Delivery in Dogs
Miao, Carol H.
Noble, Misty L.
Loeb, Keith R.
Harrang, James
Kuhr, Christian S.
Graves, Scott S.
Morrison, Kyle P.
Nichols, Timothy
Smith, Bryn
Song, Shuxian
Storb, Rainer F.
Keilman, George W.
MOLECULAR THERAPY, 2015, 23 : S107 - S107
[32] Correction of factor VIII deficiency in hemophilia A mice that target expression of a single chain variant of human factor VIII to epidermis.
Kobayashi, S
Sarkar, R
Kazazian, HH
Fakharzadeh, SS
AMERICAN JOURNAL OF HUMAN GENETICS, 2000, 67 (04) : 429 - 429
[33] Efficacy of a PEGylated variant of recombinant factor VIII in mouse models of hemophilia A
Hoellriegl, W.
Schiviz, A.
Eder, B.
Verdino, D.
Scheif-Linger, F.
Schwarz, H.
Muchitsch, E.
HAEMOPHILIA, 2012, 18 : 37 - 37
[34] INDUCTION OF TOLERANCE TO FACTOR-VIII IN HEMOPHILIA A WITH FACTOR-VIII INHIBITORS USING MODERATE DOSES OF FACTOR-VIII
WENSLEY, RT
BURN, AM
THROMBOSIS AND HAEMOSTASIS, 1983, 50 (01) : 271 - 271
[35] FACTOR-VIII SUPPLY FOR HEMOPHILIA
CARTER, J
CHAPMAN, C
FONG, R
NEW ZEALAND MEDICAL JOURNAL, 1989, 102 (870) : 326 - 326
[36] Inhibitors of Factor VIII in Hemophilia REPLY
Viel, Kevin R.
Kasper, Carol K.
Howard, Tom E.
NEW ENGLAND JOURNAL OF MEDICINE, 2009, 361 (03): : 310 - 310
[37] Factor VIII inhibitors in patients with hemophilia A
Ören, H
Yaprak, I
Irken, G
ACTA HAEMATOLOGICA, 1999, 102 (01) : 42 - 46
[38] HEMOPHILIA A - CONGENITAL DEFICIENCY OF FACTOR VIII
GRASSO, E
MINERVA PEDIATRICA, 1973, 25 (42) : 1869 - 1882
[39] Antibodies to factor VIII in hemophilia A patients
Brackmann, HH
Schwaab, R
Effenberger, W
Hess, L
Hanfland, P
Oldenburg, J
VOX SANGUINIS, 2000, 78 : 187 - 190
[40] RECOMBINANT FACTOR-VIII IN HEMOPHILIA
COHEN, A
BUTLER, R
NEW ENGLAND JOURNAL OF MEDICINE, 1991, 324 (21): : 1515 - 1516

← 1 2 3 4 5 →