Nusinersen Efficacy in Adults with Spinal Muscular Atrophy

被引：0

作者：

Day, John ^{[1
]}

Wolford, Connie ^{[2
]}

MacPherson, Chelsea ^{[4
]}

Martens, William ^{[5
]}

McDermott, Michael ^{[6
]}

Darras, Basil ^{[7
]}

De Vivo, Daryl ^{[8
]}

Cunningham, Zarazuela Zolkipli ^{[9
]}

Finkel, Richard ^{[10
]}

Sampson, Jacinda ^{[3
]}

Duong, Tina ^{[1
]}

机构：

[1] Stanford Univ, Sch Med, Palo Alto, CA 94304 USA

[2] Stanford Univ, Neurol, Stanford, CA 94305 USA

[3] Stanford Univ, Fremont, CA USA

[4] Stanford Healthcare, Rehabil, Stanford, CA USA

[5] Univ Rochester, Rochester, NY USA

[6] Rochester Univ, Rochester, NY USA

[7] Harvard Med Sch, Childrens Hosp Boston, Boston, MA USA

[8] Columbia Univ, Neurol, Boston, MA USA

[9] Childrens Hosp Philadelphia, Neurol, Philadelphia, PA 19104 USA

[10] Nemours Childrens Hosp, Orlando, FL USA

来源：

NEUROLOGY | 2018年 / 90卷

关键词：

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

S46.001

引用

页数：3

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