Impact of Inotersen on Subgroups of Patients with Hereditary TTR Amyloidosis: Results from a Double-Blind Placebo-Controlled Trial

被引:0
|
作者
Yarlas, Aaron [1 ]
Merlini, Giampaolo [2 ,3 ]
White, Michelle K. [1 ]
Kessler, Asia Sikora [1 ]
Lovley, Andrew [1 ]
Guthrie, Spencer D. [4 ]
Pollock, Michael [4 ]
Gertz, Morie A. [5 ]
机构
[1] Optum, Johnston, RI USA
[2] Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Dept Mol Med, Pavia, Italy
[3] Univ Pavia, Pavia, Italy
[4] Akcea Therapeut, Cambridge, MA USA
[5] Mayo Clin, Div Hematol, Rochester, MN USA
关键词
D O I
10.1182/blood-2018-99-119216
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
4803
引用
收藏
页数:2
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