Phase I/II gene therapy study for Chronic Granulomatous Disease: Results, lessons and perspectives

被引：1

作者：

Ott, Marion G. ^{[1
]}

Stein, Stefan ^{[2
]}

Schultze-Strasser, Stephan ^{[2
]}

Jauch, Anna ^{[3
]}

Burwinkel, Barbara ^{[4
]}

Schlegelberger, Brigitte ^{[5
]}

Goehring, Gudrun ^{[5
]}

Preiss, Carolin ^{[2
]}

Kramer, Rolf ^{[2
]}

Schwarzwaelder, Kerstin ^{[6
]}

Koehl, Ulrike ^{[7
]}

Kunkel, Hanna ^{[2
]}

Kuehlcke, Klaus ^{[8
]}

Schilz, Andrea ^{[8
]}

Schmidt, Manfred ^{[6
]}

von Kalle, Christof ^{[6
]}

Trasher, Adrian ^{[9
]}

Hoelzer, Dieter ^{[1
]}

Seger, Reinhard ^{[10
]}

Grez, Manuel ^{[2
]}

机构：

[1] Univ Frankfurt, Sch Med, Dept Hematol, Frankfurt, Germany

[2] Inst Biomed Res, Frankfurt, Germany

[3] Univ Heidelberg, Inst Human Genet, D-6900 Heidelberg, Germany

[4] German Canc Res Ctr, Div Mol Epidemiol, Heidelberg, Germany

[5] Ctr Mol Pathol, Hannover Med Sch, Hannover, Germany

[6] Univ Heidelberg, Natl Ctr Tumor Dis, D-6900 Heidelberg, Germany

[7] Univ Frankfurt, Sch Med, Dept Pediat Hematol, Frankfurt, Germany

[8] EUFETS AG, Idar Oberstein, Germany

[9] UCL, Inst Child Hlth, London WC1E 6BT, England

[10] Childrens Hosp Zurich, Div Hematol Immunol, Zurich, Switzerland

来源：

BLOOD | 2007年 / 110卷 / 11期

关键词：

D O I：

10.1182/blood.V110.11.503.503

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

503

引用

页码：155A / 155A

页数：1

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