Miglustat in Niemann-Pick disease type c (NPC)

被引：0
|
作者：
Wraith, Ed [1 ]
Vecchio, Darleen [2 ,3 ]
Prady, Helena [1 ]
Abel, Larry [4 ]
Patterson, Marc [5 ,6 ,7 ]
机构：
[1] Royal Manchester Childrens Hosp, Biochem Genet Unit, Manchester M27 1HA, Lancs, England
[2] Columbia Univ, Dept Neurol, New York, NY 10027 USA
[3] Columbia Univ, Dept Pediat, New York, NY 10027 USA
[4] Univ Melbourne, Dept Optometry & Vis Sci, Parkville, Vic 3052, Australia
[5] Mayo Clin, Dept Neurol, Rochester, MN USA
[6] Mayo Clin, Dept Pediat & Adolescent Med, Rochester, MN USA
[7] Mayo Clin, Dept Med Genet, Rochester, MN USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2008年 / 93卷 / 02期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
111
引用
收藏
页码：S43 / S43
页数：1
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