Gene therapy and rare diseases

被引:2
|
作者
Cohen-Haguenauer, O. [1 ,2 ]
机构
[1] Ecole Normale Super, LBPA, F-94235 Cachan, France
[2] Univ Paris 07, Hop St Louis, F-75475 Paris 10, France
来源
REVUE DE MEDECINE INTERNE | 2011年 / 32卷
关键词
Gene therapy; Rare diseases;
D O I
10.1016/j.revmed.2011.09.015
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
[No abstract available]
引用
收藏
页码:S210 / S212
页数:3
相关论文
共 50 条
  • [31] Will Gene Editing Orphanize Rare Diseases?
    Mann, Douglas L.
    JACC-BASIC TO TRANSLATIONAL SCIENCE, 2023, 8 (01): : 106 - 107
  • [32] Curative gene therapies for rare diseases
    Rocio Maldonado
    Sami Jalil
    Kirmo Wartiovaara
    Journal of Community Genetics, 2021, 12 : 267 - 276
  • [33] What may be the impact of new technologies for rare diseases? Focus on gene and cell therapy
    Peschanski, Marc
    PRESSE MEDICALE, 2010, 39 (05): : 64 - 66
  • [34] Gene Therapy in Rare Respiratory Diseases: What Have We Learned So Far?
    Banuls, Lucia
    Pellicer, Daniel
    Castillo, Silvia
    Mercedes Navarro-Garcia, Maria
    Magallon, Maria
    Gonzalez, Cruz
    Dasi, Francisco
    JOURNAL OF CLINICAL MEDICINE, 2020, 9 (08) : 1 - 29
  • [35] The Impact of Rare Diseases and Drug Therapy
    Kvancz, David A.
    AMERICAN JOURNAL OF PHARMACY BENEFITS, 2016, 8 (04) : 128 - 132
  • [36] Individualized ASO therapy for rare diseases
    Aartsma-Rus, Annemieke
    COMMUNICATIONS MEDICINE, 2023, 3 (01):
  • [37] Individualized ASO therapy for rare diseases
    Communications Medicine, 3
  • [38] Gene Therapy for Liver Diseases
    George Wu
    Catherine H Wu
    肝脏, 2002, (S1) : 2 - 3
  • [39] Gene therapy for cardiovascular diseases
    Elizabeth G. Nabel
    Journal of Nuclear Cardiology, 1999, 6 : 69 - 75
  • [40] Gene therapy for acute diseases
    Factor, P
    MOLECULAR THERAPY, 2001, 4 (06) : 515 - 524