Results of a family survey on healthcare resource needs in children with neuronal ceroid lipofuscinosis type 2 (CLN2) disease in the US and Canada

被引：0

作者：

Rastogi, Sarang ^{[1
]}

Conner, Therese ^{[2
]}

Cook, Francesca ^{[1
]}

Fernandez, Vivian ^{[1
]}

Kirby, Tracy ^{[3
]}

机构：

[1] REGENXBIO Inc, Rockville, MD USA

[2] Xcenda, Palm Harbor, FL USA

[3] BDSRA, Columbus, OH USA

来源：

MOLECULAR GENETICS AND METABOLISM | 2020年 / 129卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2019.11.354

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

345

引用

页码：S135 / S135

页数：1

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