Efficacy and safety with >3 years of inotersen treatment for the polyneuropathy of hereditary transthyretin amyloidosis

被引：0

作者：

Coelho, Teresa ^{[1
]}

Whelan, Carol ^{[2
]}

Conceicao, Isabel ^{[3
,4
]}

Brannagan, Thomas ^{[5
]}

Wang, Annabel ^{[6
]}

Polydefkis, Michael ^{[7
]}

Dyck, Peter ^{[8
]}

Plante-Bordeneuve, Violaine ^{[9
]}

Berk, John ^{[10
]}

Merlini, Giampaolo ^{[11
]}

Obici, Laura ^{[11
]}

Drachman, Brian ^{[12
]}

Gorevic, Peter ^{[13
]}

Schmidt, Hartmut ^{[14
]}

Plana, Josep Maria Campistol ^{[15
]}

Gamez, Josep ^{[16
]}

Kristen, Arnt ^{[17
]}

Mazzeo, Anna ^{[18
]}

Narayana, Arvind ^{[19
]}

Olugemo, Kemi ^{[20
]}

Aquino, Peter ^{[21
]}

Benson, Merrill ^{[22
]}

Gertz, Morie ^{[23
]}

机构：

[1] Ctr Hosp Univ Porto, Dept Neurophysiol, Porto, Portugal

[2] Royal Free Hosp, Natl Amyloidosis Ctr, London, England

[3] CHULN, Hosp Santa Maria, Lisbon, Portugal

[4] Univ Lisbon, Dept Neurosci, Fac Med, Lisbon, Portugal

[5] Columbia Univ, Med Ctr, Peripheral Neuropathy Ctr, New York, NY USA

[6] Univ Calif Irvine, Dept Neurol, Orange, CA 92668 USA

[7] Johns Hopkins Univ, Dept Neurol, Baltimore, MD 21218 USA

[8] Mayo Clin, Peripheral Nerve Res Lab, Rochester, MN USA

[9] CHU Henri Mondor, Dept Neurol, Creteil, France

[10] Boston Univ, Amyloidosis Ctr, Boston, MA 02215 USA

[11] IRCCS Fdn Policlin San Matteo, Amyloidosis Ctr, Pavia, Italy

[12] Penn Presbyterian Med Ctr, Dept Cardiovasc Med, Philadelphia, PA USA

[13] Mt Sinai Med Ctr, Dept Rheumatol, New York, NY 10029 USA

[14] Muenster Univ Hosp, Dept Gastroenterol Hepatol Endocrinol Diabetol &, Munster, Germany

[15] Univ Barcelona, Inst Invest Biomed August Pi i Sunyer, Hosp Clin, Barcelona, Spain

[16] Hosp Univ Vall dHebron, Dept Neurol, Barcelona, Spain

[17] Heidelberg Univ Hosp, Amyloidosis Ctr, Heidelberg, Germany

[18] Univ Messina, Dept Neurol, Messina, Italy

[19] Akcea Therapeut, Global Med Affairs, Boston, MA USA

[20] Akcea Therapeut, Clin Dev, Boston, MA USA

[21] Akcea Therapeut, Global Drug Safety & Pharmacovigilance, Boston, MA USA

[22] Indiana Univ Sch Med, Dept Pathol & Lab Med, Indianapolis, IN 46202 USA

[23] Mayo Clin, Bone Marrow Transplant Program, Rochester, MN USA

来源：

JOURNAL OF THE NEUROLOGICAL SCIENCES | 2021年 / 429卷

关键词：

D O I：

10.1016/j.jns.2021.117867

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

117867

引用

页数：3

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Efficacy and safety with &gt;3 years of inotersen treatment for the polyneuropathy of hereditary transthyretin amyloidosis

Efficacy and safety with >3 years of inotersen treatment for the polyneuropathy of hereditary transthyretin amyloidosis