Newborn Screening for Spinal Muscular Atrophy and Lysosomal Storage Disorders Takes Advantage of Novel Therapies

被引:1
|
作者
Andersson, Hans C. [1 ]
机构
[1] Tulane Univ, Med Sch, Hayward Genet Ctr, 1403 Tulane Ave, New Orleans, LA 70118 USA
来源
JOURNAL OF PEDIATRICS | 2017年 / 190卷
关键词
D O I
10.1016/j.jpeds.2017.08.016
中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
引用
收藏
页码:9 / 10
页数:3
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