A High-Throughput Screening Approach to Identify Therapeutics for the Treatment of Diamond-Blackfan Anaemia

被引:0
|
作者
Villacis, Lorena Nunez [1 ]
Al-Obaidi, Sheren J. [1 ]
Madhamshettiwar, Piyush [2 ]
Hein, Nadine [1 ]
Chen, Jun [3 ]
Soo, Priscilla [1 ]
Poh, Perlita [1 ]
Pavy, Megan [1 ]
Simpson, Kaylene J. [2 ,4 ]
Gonda, Thomas John [5 ]
Pearson, Richard B. [4 ,6 ,7 ,8 ,9 ]
Flygare, Johan [9 ]
Hannan, Katherine M. [1 ,7 ]
George, Amee J. [1 ,2 ,10 ,11 ,12 ]
Hannan, Ross [1 ,4 ,6 ,7 ,8 ,11 ]
机构
[1] Australian Natl Univ, ACRF Dept Canc Biol & Therapeut, Canberra, ACT, Australia
[2] Peter MacCallum Canc Ctr, Victorian Ctr Funct Genom, Melbourne, Vic, Australia
[3] Lund Univ, Lund, Sweden
[4] Univ Melbourne, Sir Peter MacCallum Dept Oncol, Melbourne, Vic, Australia
[5] Univ Queensland, Pharm Australia Ctr Excellence, Brisbane, Qld, Australia
[6] Peter MacCallum Canc Ctr, Oncogen Signalling & Growth Control Program, Melbourne, Vic, Australia
[7] Univ Melbourne, Dept Biochem & Mol Biol, Melbourne, Vic, Australia
[8] Monash Univ, Dept Biochem & Mol Biol, Melbourne, Vic, Australia
[9] Lund Univ, Lund Strateg Ctr Stem Cell Biol, Mol Med & Gene Therapy, Lund, Sweden
[10] Australian Natl Univ, ANU Ctr Therapeut Discovery, Canberra, ACT, Australia
[11] Univ Queensland, Sch Biomed Sci, Brisbane, Qld, Australia
[12] Univ Melbourne, Dept Clin Pathol, Melbourne, Vic, Australia
关键词
D O I
10.1182/blood-2018-99-114303
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
3859
引用
收藏
页数:3
相关论文
共 50 条
  • [41] CYCLOSPORINE-A TREATMENT FOR DIAMOND-BLACKFAN ANEMIA
    SPLAIN, J
    BERMAN, BW
    AMERICAN JOURNAL OF HEMATOLOGY, 1992, 39 (03) : 208 - 211
  • [42] ORAL MEGADOSE METHYLPREDNISOLONE FOR THE TREATMENT OF DIAMOND-BLACKFAN ANEMIA
    OZSOYLU, S
    PEDIATRIC HEMATOLOGY AND ONCOLOGY, 1994, 11 (05) : 561 - 562
  • [43] Diamond-Blackfan Anemia: Diagnosis, Treatment, and Molecular Pathogenesis
    Lipton, Jeffrey M.
    Ellis, Steven R.
    HEMATOLOGY-ONCOLOGY CLINICS OF NORTH AMERICA, 2009, 23 (02) : 261 - +
  • [44] Diamond-Blackfan anemia - Natural history and sequelae of treatment
    Janov, AJ
    Leong, T
    Nathan, DG
    Guinan, EC
    MEDICINE, 1996, 75 (02) : 77 - 87
  • [45] Pregnancy in bone marrow failure syndromes: Diamond-Blackfan anaemia and Shwachman-Diamond syndrome
    Alter, BP
    Kumar, M
    Lockhart, LL
    Sprinz, PG
    Rowe, TF
    BRITISH JOURNAL OF HAEMATOLOGY, 1999, 107 (01) : 49 - 54
  • [46] HIGH-DOSE DESFEROXAMINE AND DIAMOND-BLACKFAN ANEMIA
    KANZ, L
    ARNOLD, H
    LOHR, GW
    ANNALS OF INTERNAL MEDICINE, 1986, 104 (04) : 585 - 586
  • [47] CLINICAL AND GENETIC DIVERSITY IN DIAMOND-BLACKFAN ANAEMIA: AN UPDATE FROM THE UNITED KINGDOM
    Iskander, D.
    Miller, C.
    Alikian, M.
    Harrington, Y.
    Al-Oqaily, Q.
    Roberts, I.
    Karadimitris, A.
    de la Fuente, J.
    HAEMATOLOGICA, 2017, 102 : 63 - 63
  • [48] ORAL MEGADOSE METHYLPREDNISOLONE FOR TREATMENT OF DIAMOND-BLACKFAN ANEMIA
    OZSOYLU, S
    BRITISH JOURNAL OF HAEMATOLOGY, 1992, 81 (01) : 135 - 136
  • [49] Development of High-Throughput Screening Assay for Antihantaviral Therapeutics
    Roy, Anuradha
    Mir, Mohammad A.
    SLAS DISCOVERY, 2017, 22 (06) : 767 - 774
  • [50] Understanding complex disease-related mechanisms: Rational therapies for Diamond-Blackfan anaemia
    Lipton, Jeffrey M.
    BRITISH JOURNAL OF HAEMATOLOGY, 2024, 204 (05) : 1598 - 1599