AAV-CRISPR/Cas9 Gene Editing is Therapeutic in a Novel, Humanized Mouse Model of GUCY2D-Associated Cone Rod Dystrophy (CORD6)

被引：0
|
作者：
Mellen, Russell W. [1 ]
McCullough, K. Tyler [1 ]
Fajardo, Diego [1 ]
Calabro, Kaitlyn [1 ]
Crosson, Sean [1 ]
Xu, Emily [1 ]
Boye, Sanford L. [1 ]
Boye, Shannon E. [2 ]
机构：
[1] Univ Florida, Dept Pediat, Gainesville, FL USA
[2] Univ Florida, Dept Pediat, Div Cellular & Mol Therapy, Gainesville, FL USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1216
引用
收藏
页码：566 / 566
页数：1
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