Preclinical development of a TALEN®-based genome editing therapy for RAG1 deficiency

被引：0
|
作者：
Rhiel, M. [1 ,2 ]
Klermund, J. [1 ,2 ]
Jullierat, A. [3 ]
Andrieux, G. [4 ,5 ,6 ]
Rositzka, J. [1 ,2 ]
Duchateau, P. [7 ]
Cathomen, T. [1 ,2 ]
Cornu, T. I. [1 ,2 ]
机构：
[1] Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, D-79106 Freiburg, Germany
[2] Univ Freiburg, Ctr Chron Immunodeficiency CCI, Med Ctr, D-79106 Freiburg, Germany
[3] Cellectis Inc, New York, NY 10016 USA
[4] Univ Freiburg, Inst Med Bioinformat & Syst Med, Med Ctr, D-79110 Freiburg, Germany
[5] German Canc Consortium DKTK, D-79106 Freiburg, Germany
[6] Partner Site Freiburg, German Canc Res Ctr DKFZ, D-79106 Freiburg, Germany
[7] Cellectis SA, F-75013 Paris, France
来源：
HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
OR34
引用
收藏
页码：A13 / A14
页数：2
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