Neurosteroid treatment of lysosomal storage disorders

被引:0
|
作者
Mellon, Synthia [1 ]
Gong, Wenhui [1 ]
机构
[1] Univ Calif San Francisco, San Francisco, CA 94143 USA
关键词
D O I
10.1016/j.ymgme.2008.11.089
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
88
引用
收藏
页码:S31 / S31
页数:1
相关论文
共 50 条
  • [41] New treatments for lysosomal storage disorders
    Wilmott, RW
    JOURNAL OF PEDIATRICS, 2004, 144 (05): : 2A - 2A
  • [42] Gene therapy for the lysosomal storage disorders
    Cabrera-Salazar, MA
    Novelli, E
    Barranger, JA
    CURRENT OPINION IN MOLECULAR THERAPEUTICS, 2002, 4 (04) : 349 - 358
  • [43] Lysosomal storage disorders: Present and future
    Phadke, Shubha R.
    INDIAN PEDIATRICS, 2015, 52 (12) : 1025 - 1026
  • [44] Symposium on lysosomal storage disorders - Introduction
    Grabowski, GA
    JOURNAL OF PEDIATRICS, 2004, 144 (05): : S1 - S1
  • [45] Gene therapy for lysosomal storage disorders
    Cartier, Nathalie
    HUMAN GENE THERAPY, 2010, 21 (10) : 1360 - 1360
  • [46] Newborn Screening for Lysosomal Storage Disorders
    Anderson, Sharon
    JOURNAL OF PEDIATRIC HEALTH CARE, 2018, 32 (03) : 285 - 294
  • [47] Newborn screening for lysosomal storage disorders
    Meikle, Peter J.
    Grasby, Dallas J.
    Dean, Caroline J.
    Lang, Debbie L.
    Bockmann, Michelle
    Whittle, Alison M.
    Fietz, Michael J.
    Simonsen, Henrik
    Fuller, Maria
    Brooks, Douglas A.
    Hopwood, John J.
    MOLECULAR GENETICS AND METABOLISM, 2006, 88 (04) : 307 - 314
  • [48] Newborn screening for lysosomal storage disorders
    Matern, Dietrich
    ACTA PAEDIATRICA, 2008, 97 : 33 - 37
  • [49] A block of autophagy in lysosomal storage disorders
    Settembre, Carmine
    Fraldi, Alessandro
    Jahreiss, Luca
    Spampanato, Carmine
    Venturi, Consuelo
    Medina, Diego
    de Pablo, Raquel
    Tacchetti, Carlo
    Rubinsztein, David C.
    Ballabio, Andrea
    HUMAN MOLECULAR GENETICS, 2008, 17 (01) : 119 - 129
  • [50] Newborn screening for lysosomal storage disorders
    Millington, DS
    CLINICAL CHEMISTRY, 2005, 51 (05) : 808 - 809