UNRAVELING THE MECHANISM OF VX-770 ON WTAND G551D-CFTR

被引:0
|
作者
Lin, W. [1 ]
Jih, K. [1 ]
Hwang, T. [1 ]
机构
[1] Univ Missouri, Columbia, MO USA
关键词
D O I
暂无
中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
引用
收藏
页码:210 / 210
页数:1
相关论文
共 50 条
  • [21] VX-809 AND VX-770 TREATMENT IN RECTAL CF ORGANOIDS EXPRESSING UNCOMMON CFTR GENOTYPES
    Dekkers, F.
    Kruisselbrink, E.
    de Jonge, H.
    Bronsveld, I
    de Winter, K.
    Janssens, H.
    Clevers, H.
    van der Ent, K.
    Vijftigschild, L.
    PEDIATRIC PULMONOLOGY, 2013, 48 : 269 - 269
  • [22] VX-770 AND VX-809 ENHANCE CFTR CHANNEL FUNCTION IN THE NATIVE HUMAN SWEAT DUCT
    Reddy, M.
    Shamsuddin, A.
    Quinton, P. M.
    PEDIATRIC PULMONOLOGY, 2016, 51 : 212 - 212
  • [23] ADDITION OF VX-661, AN INVESTIGATIONAL CFTR CORRECTOR, TO IVACAFTOR, A CFTR POTENTIATOR, IN PATIENTS WITH CF AND HETEROZYGOUS FOR F508DEL/G551D-CFTR
    Donaldson, S. H.
    Pilewski, J. M.
    Cooke, J.
    Himes-Lekstrom, J.
    PEDIATRIC PULMONOLOGY, 2014, 49 : 308 - 309
  • [24] Pseudomonas aeruginosa in Cystic Fibrosis Patients With G551D-CFTR Treated With Ivacaftor
    Heltshe, Sonya L.
    Mayer-Hamblett, Nicole
    Burns, Jane L.
    Khan, Umer
    Baines, Arthur
    Ramsey, Bonnie W.
    Rowe, Steven M.
    CLINICAL INFECTIOUS DISEASES, 2015, 60 (05) : 703 - 712
  • [25] Identifying the molecular target sites for CFTR potentiators GLPG1837 and VX-770
    Yeh, Han-, I
    Qiu, Liming
    Sohma, Yoshiro
    Conrath, Katja
    Zou, Xiaoqin
    Hwang, Tzyh-Chang
    JOURNAL OF GENERAL PHYSIOLOGY, 2019, 151 (07): : 912 - 928
  • [26] VX-770 IN SUBJECTS WITH CF AND HOMOZYGOUS FOR THE F508DEL-CFTR MUTATION
    Flume, P. A.
    Borowitz, D.
    Liou, T.
    Li, H.
    Yen, K.
    Ordonez, C.
    Geller, D. E.
    PEDIATRIC PULMONOLOGY, 2011, : 284 - 285
  • [27] Synthesis of 1,2,3-triazole analogs of CFTR potentiator VX-770
    Ody, Britton
    ABSTRACTS OF PAPERS OF THE AMERICAN CHEMICAL SOCIETY, 2019, 257
  • [28] Rescue of CF airway epithelial cell function in vitro by a CFTR potentiator, VX-770
    Van Goor, Fredrick
    Hadida, Sabine
    Grootenhuis, Peter D. J.
    Burton, Bill
    Cao, Dong
    Neuberger, Tim
    Turnbull, Amanda
    Singh, Ashvani
    Joubran, John
    Hazlewood, Anna
    Zhou, Jinglan
    McCartney, Jason
    Arumugam, Vijayalaksmi
    Decker, Caroline
    Yang, Jennifer
    Young, Chris
    Olson, Eric R.
    Wine, Jeffery J.
    Frizzell, Raymond A.
    Ashlock, Melissa
    Negulescu, Paul
    PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2009, 106 (44) : 18825 - 18830
  • [29] Population pharmacokinetics and pharmacodynamics of the CFTR potentiator ivacaftor in patients with cystic fibrosis and a G551D-CFTR mutation
    Haseltine, Eric
    Mondick, John
    Garg, Varun
    Lekstrom-Himes, Julie
    JOURNAL OF PHARMACOKINETICS AND PHARMACODYNAMICS, 2017, 44 : S30 - S31
  • [30] Mechanism of G551D-CFTR (cystic fibrosis transmembrane conductance regulator) potentiation by a high affinity ATP analog
    Bompadre, Silvia G.
    Li, Min
    Hwang, Tzyh-Chang
    JOURNAL OF BIOLOGICAL CHEMISTRY, 2008, 283 (09) : 5364 - 5369