Multiple Novel Engineered AAV Capsids Demonstrate Enhanced Brain and Spinal Cord Gene Transfer after Systemic Administration in Adult Mice

被引：0
|
作者：
Murlidharan, Giridhar [1 ]
Wang, Hongxing [1 ]
Adachi, Kei [1 ]
Christensen, Emily [1 ]
Thompson, Jeff [1 ]
Felix-Ortiz, Ada [1 ]
Goulet, Martin [1 ]
Tam Nguyen [1 ]
Johnson, Brianna [1 ]
Liu, Li [1 ]
Zhou, Joice [1 ]
Paranjpe, Maneesha [1 ]
Chung, Charlotte [1 ]
Aubin, Justin [1 ]
Sah, Dinah [1 ]
Carter, Todd [1 ]
Hou, Jay [1 ]
机构：
[1] Voyager Therapeut, Cambridge, MA USA
来源：
MOLECULAR THERAPY | 2019年 / 27卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
240
引用
收藏
页码：119 / 119
页数：1
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