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- [31] Progression of Hip Dysplasia in Mucopolysaccharidosis Type I Hurler After Successful Hematopoietic Stem Cell TransplantationJOURNAL OF BONE AND JOINT SURGERY-AMERICAN VOLUME, 2016, 98 (05): : 386 - 395Langereis, Eveline J.论文数: 0 引用数: 0 h-index: 0机构: Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlandsden Os, Matthijs M.论文数: 0 引用数: 0 h-index: 0机构: Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsBreen, Catherine论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, NHS Fdn Trust, Cent Manchester Univ Hosp, Genet Med,Manchester Acad Hlth Sci Ctr, Manchester M13 0JH, Lancs, England Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsJones, Simon A.论文数: 0 引用数: 0 h-index: 0机构: Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsKnaven, Olga C.论文数: 0 引用数: 0 h-index: 0机构: Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands St Marys Hosp, NHS Fdn Trust, Cent Manchester Univ Hosp, Genet Med,Manchester Acad Hlth Sci Ctr, Manchester M13 0JH, Lancs, England Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsMercer, Jean论文数: 0 引用数: 0 h-index: 0机构: Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsMiller, Weston P.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Childrens Hosp, Div Pediat Blood & Marrow Transplantat, Minneapolis, MN USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsKelly, Paula M.论文数: 0 引用数: 0 h-index: 0机构: Our Ladys Childrens Hosp, Dept Orthopaed Surg, Dublin, Ireland Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsKennedy, Jim论文数: 0 引用数: 0 h-index: 0机构: Our Ladys Childrens Hosp, Dept Orthopaed Surg, Dublin, Ireland Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsKetterl, Tyler G.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Childrens Hosp, Div Pediat Blood & Marrow Transplantat, Minneapolis, MN USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsO'Meara, Anne论文数: 0 引用数: 0 h-index: 0机构: Our Ladys Childrens Hosp, Natl HSCT Dept, Dublin, Ireland Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsOrchard, Paul J.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Childrens Hosp, Div Pediat Blood & Marrow Transplantat, Minneapolis, MN USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsLund, Troy C.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Childrens Hosp, Div Pediat Blood & Marrow Transplantat, Minneapolis, MN USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlandsvan Rijn, Rick R.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Radiol, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsSakkers, Ralph J.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Utrecht, Dept Orthopaed Surg, Utrecht, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsWhite, Klane K.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Seattle Childrens Hosp, Dept Orthoped & Sports Med, Seattle, WA 98195 USA Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, NetherlandsWijburg, Frits A.论文数: 0 引用数: 0 h-index: 0机构: Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands Emma Childrens Hosp, Dept Pediat Metab Dis, Amsterdam, Netherlands
- [32] Growth patterns in children with mucopolysaccharidosis type I-Hurler after hematopoietic stem cell transplantation: Comparison with untreated patientsMOLECULAR GENETICS AND METABOLISM REPORTS, 2021, 28论文数: 引用数: h-index:机构:Chiaraluce, Sofia论文数: 0 引用数: 0 h-index: 0机构: Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, ItalyGasperini, Serena论文数: 0 引用数: 0 h-index: 0机构: Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, ItalyMolinari, Silvia论文数: 0 引用数: 0 h-index: 0机构: Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy论文数: 引用数: h-index:机构:Rovelli, Attilio论文数: 0 引用数: 0 h-index: 0机构: Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy Univ Milano Bicocca, Azienda Osped San Gerardo, Fdn Monza & Brianza Bambino & Mamma, Dept Pediat, Monza, MB, Italy论文数: 引用数: h-index:机构:
- [33] Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedureORPHANET JOURNAL OF RARE DISEASES, 2011, 6de Ru, Minke H.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsBoelens, Jaap J.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Utrecht, Dept Pediat, Pediat Blood & Marrow Transplantat Program, Utrecht, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsDas, Anibh M.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat, Clin Kidney Liver & Metab Dis, D-3000 Hannover, Germany Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsJones, Simon A.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, St Marys Hosp, Cent Manchester Univ Hosp NHS Fdn Trust, Manchester Acad Hlth Sci Ctr, Manchester M13 0JH, Lancs, England Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlandsvan der Lee, Johanna H.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Pediat Clin Epidemiol, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsMahlaoui, Nizar论文数: 0 引用数: 0 h-index: 0机构: Necker Enfants Malad Hosp, AP HP, Pediat Immunol Hematol Unit, Paris, France Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsMengel, Eugen论文数: 0 引用数: 0 h-index: 0机构: Johannes Gutenberg Univ Mainz, Childrens Hosp, D-6500 Mainz, Germany Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsOffringa, Martin论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Pediat Clin Epidemiol, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsO'Meara, Anne论文数: 0 引用数: 0 h-index: 0机构: Our Ladys Childrens Hosp, Dept Haematol Oncol, Dublin, Ireland Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsParini, Rossella论文数: 0 引用数: 0 h-index: 0机构: San Gerardo Hosp, Dept Pediat, Rare Metab Dis Unit, Monza, Italy Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsRovelli, Attilio论文数: 0 引用数: 0 h-index: 0机构: San Gerardo Hosp, Dept Pediat, Bone Marrow Transplant Unit, Monza, Italy Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsSykora, Karl-Walter论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Dept Pediat Hematol Oncol, D-3000 Hannover, Germany Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsValayannopoulos, Vassili论文数: 0 引用数: 0 h-index: 0机构: Necker Enfants Malad Hosp, Reference Ctr Inherited Metab Disorders, Paris, France Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsVellodi, Ashok论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Sick Children, Metab Unit, London WC1N 3JH, England Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsWynn, Robert F.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Dept Blood & Marrow Transplant, Manchester M27 1HA, Lancs, England Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsWijburg, Frits A.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Amsterdam Lysosome Ctr Sphinx, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands
- [34] Treatment of hip dysplasia in patients with mucopolysaccharidosis type I after hematopoietic stem cell transplantation: results of an international consensus procedureORPHANET JOURNAL OF RARE DISEASES, 2013, 8Langereis, Eveline J.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Lysosome Ctr Sphinx, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsBorgo, Andrea论文数: 0 引用数: 0 h-index: 0机构: Univ Padua, Dept Orthopaed & Traumatol, Padua, Italy Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsCrushell, Ellen论文数: 0 引用数: 0 h-index: 0机构: Childrens Univ Hosp, Natl Ctr Inherited Metab Disorders, Dublin, Ireland Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsHarmatz, Paul R.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp & Res Ctr Oakland, Oakland, CA USA Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlandsvan Hasselt, Peter M.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Utrecht, Dept Pediat, Utrecht, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsJones, Simon A.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, NHS Fdn Trust, Cent Manchester Univ Hosp, Manchester Acad Hlth Sci Ctr, Manchester, Lancs, England Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsKelly, Paula M.论文数: 0 引用数: 0 h-index: 0机构: Our Ladys Childrens Hosp, Dept Orthopaed Surg, Dublin, Ireland Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsLampe, Christina论文数: 0 引用数: 0 h-index: 0机构: Johannes Gutenberg Univ Mainz, Univ Med Ctr, Dept Pediat & Adolescent Med, Mainz, Germany Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlandsvan der Lee, Johanna H.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Clin Res Unit, Woman Child Ctr, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsOdent, Thierry论文数: 0 引用数: 0 h-index: 0机构: Paris Descartes Univ, Necker Enfants Malades Hosp, Dept Orthopaed Surg, Paris, France Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsSakkers, Ralph论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Utrecht, Dept Orthopaed Surg, Utrecht, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsScarpa, Maurizio论文数: 0 引用数: 0 h-index: 0机构: Univ Padua, Dept Pediat, Padua, Italy Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsSchafroth, Matthias U.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Orthopaed Surg, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsStruijs, Peter A.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Orthopaed Surg, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsValayannopoulos, Vassili论文数: 0 引用数: 0 h-index: 0机构: IMAGINE Inst, Paris, France Paris Descartes Univ, Reference Ctr Inherited Metab Dis, Necker Enfants Malades Hosp, Paris, France Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsWhite, Klane K.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Dept Orthoped & Sports Med, Seattle Childrens Hosp, Seattle, WA 98195 USA Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, NetherlandsWijburg, Frits A.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Lysosome Ctr Sphinx, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Pediat, NL-1105 AZ Amsterdam, Netherlands
- [35] Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedureOrphanet Journal of Rare Diseases, 6Minke H de Ru论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterJaap J Boelens论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterAnibh M Das论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterSimon A Jones论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterJohanna H van der Lee论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterNizar Mahlaoui论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterEugen Mengel论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterMartin Offringa论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterAnne O'Meara论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterRossella Parini论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterAttilio Rovelli论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterKarl-Walter Sykora论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterVassili Valayannopoulos论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterAshok Vellodi论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterRobert F Wynn论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical CenterFrits A Wijburg论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Amsterdam Lysosome Center 'Sphinx', Academic Medical Center
- [36] Treatment of hip dysplasia in patients with mucopolysaccharidosis type I after hematopoietic stem cell transplantation: results of an international consensus procedureOrphanet Journal of Rare Diseases, 8Eveline J Langereis论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterAndrea Borgo论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterEllen Crushell论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterPaul R Harmatz论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterPeter M van Hasselt论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterSimon A Jones论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterPaula M Kelly论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterChristina Lampe论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterJohanna H van der Lee论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterThierry Odent论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterRalph Sakkers论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterMaurizio Scarpa论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterMatthias U Schafroth论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterPeter A Struijs论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterVassili Valayannopoulos论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterKlane K White论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical CenterFrits A Wijburg论文数: 0 引用数: 0 h-index: 0机构: University of Amsterdam,Department of Pediatrics and Lysosome Center 'Sphinx’, Academic Medical Center
- [37] A novel preclinical model of mucopolysaccharidosis type II for developing human hematopoietic stem cell gene therapyGene Therapy, 2023, 30 : 288 - 296Yohta Shimada论文数: 0 引用数: 0 h-index: 0机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical SciencesNatsumi Ishii论文数: 0 引用数: 0 h-index: 0机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical SciencesTakashi Higuchi论文数: 0 引用数: 0 h-index: 0机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical SciencesMotohito Goto论文数: 0 引用数: 0 h-index: 0机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical SciencesToya Ohashi论文数: 0 引用数: 0 h-index: 0机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical SciencesHiroshi Kobayashi论文数: 0 引用数: 0 h-index: 0机构: The Jikei University School of Medicine,Division of Gene Therapy, Research Center for Medical Sciences
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