Improved Lentiviral In Vivo Gene Therapy for Chronic Granulomatous Disease

被引：0
|
作者：
Yuan, Haokun [1 ]
Liu, Hongwei [1 ]
Wu, Xiaomei [1 ]
Liu, Yuchen [2 ]
Zhang, Rui [2 ]
Chang, Lung-Ji [1 ,2 ]
机构：
[1] Univ Elect Sci & Technol China, Sch Med, Chengdu, Peoples R China
[2] Genoimmune Med Inst, Shenzhen, Peoples R China
来源：
BLOOD | 2022年 / 140卷
关键词：
D O I：
10.1182/blood-2022-159862
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：4921 / 4922
页数：2
相关论文
共 50 条
  • [21] Gene therapy of chronic granulomatous disease
    Grez, M
    Becker, S
    Saulnier, S
    Knöss, H
    Ott, MG
    Maurer, A
    Dinauer, MC
    Hoelzer, D
    Seger, R
    Hossle, JP
    BONE MARROW TRANSPLANTATION, 2000, 25 (Suppl 2) : S99 - S104
  • [22] Lineage- and stage-restricted lentiviral vectors for the gene therapy of chronic granulomatous disease
    I Barde
    E Laurenti
    S Verp
    M Wiznerowicz
    S Offner
    A Viornery
    A Galy
    A Trumpp
    D Trono
    Gene Therapy, 2011, 18 : 1087 - 1097
  • [23] Lineage- and stage-restricted lentiviral vectors for the gene therapy of chronic granulomatous disease
    Barde, I.
    Laurenti, E.
    Verp, S.
    Wiznerowicz, M.
    Offner, S.
    Viornery, A.
    Galy, A.
    Trumpp, A.
    Trono, D.
    GENE THERAPY, 2011, 18 (11) : 1087 - 1097
  • [24] Correction of p47-phox deficient Chronic Granulomatous Disease by lentiviral gene therapy
    Schejtman, Andrea
    Cutrim Aragao Filho, W.
    Clare, S.
    Weisser, M.
    Zinicola, M.
    Booth, C.
    Burns, S. O.
    Siler, U.
    Reichenbach, J.
    Gaspar, H. B.
    Thomas, D.
    Condino-Neto, A.
    Thrasher, A. J.
    Santilli, G.
    HUMAN GENE THERAPY, 2018, 29 (07) : A12 - A12
  • [25] Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatous Disease
    Farinelli, Giada
    Chiriaco, Maria
    Capo, Valentina
    Zonari, Erika
    Migliavacca, Maddalena
    Hernandez, Raisa Jofra
    Scaramuzza, Samantha
    Di Matteo, Gigliola
    Sergi, Lucia Sergi
    Rossi, Alice
    Ranucci, Serena
    Bragonzi, Alessandra
    Kajaste-Rudnitski, Anna
    Trono, Didier
    Grez, Manuel
    Rossi, Paolo
    Finocchi, Andrea
    Naldini, Luigi
    Gentner, Bernhard
    Aiuti, Alessandro
    MOLECULAR THERAPY, 2015, 23 : S115 - S116
  • [26] Dual-Regulated Lentiviral Vector for Gene Therapy of X-linked Chronic Granulomatous Disease
    Farinelli, G.
    Chiriaco, M.
    Capo, V.
    Zonari, E.
    Migliavacca, M.
    Hernandez, R. Jofra
    Scaramuzza, S.
    Di Matteo, G.
    Sergi, L. Sergi
    Kajaste-Rudnitski, A.
    Trono, D.
    Grez, M.
    Rossi, P.
    Finocchi, A.
    Naldini, L.
    Gentner, B.
    Aiuti, A.
    HUMAN GENE THERAPY, 2014, 25 (11) : A26 - A26
  • [27] Dual-regulated lentiviral vector for gene therapy of x-linked chronic granulomatous disease
    Farinelli, G.
    Hernandez, R. Jofra
    Migliavacca, M.
    Zonari, E.
    Capo, V.
    Chiriaco, M.
    Scaramuzza, S.
    Di Matteo, G.
    Sergi, L. Sergi
    Rossi, A.
    Ranucci, S.
    Bragonzi, A.
    Kajaste-Rudnitski, A.
    Trono, D.
    Grez, M.
    Rossi, P.
    Finocchi, A.
    Naldini, L.
    Gentner, B.
    Aiuti, A.
    HUMAN GENE THERAPY, 2015, 26 (10) : A51 - A51
  • [28] Lentiviral Vector Gene Therapy for X-linked Chronic Granulomatous Disease Corrects Neutrophil Function
    Malech, Harry L.
    Booth, Claire
    Kang, Elizabeth M.
    Pai, Sung-Yun
    Shaw, Kit L.
    Santilli, Giorgia
    Armant, Myriam
    Buckland, Karen F.
    Choi, Uimook
    De Ravin, Suk See
    Dorsey, Morna J.
    Kuo, Caroline Y.
    Leon-Rico, Diego
    Rivat, Christine
    Snell, Katie
    Xu-Bayford, Jinhua
    Morris, Emma C.
    Terrazas, Dayna
    Wang, Leo D.
    Honnet, Geraldine
    Newburger, Peter
    Bushman, Frederic D.
    Grez, Manuel
    Gaspar, Bobby
    Williams, David A.
    Galy, Anne
    Kohn, Donald B.
    Thrasher, Adrian J.
    JOURNAL OF CLINICAL IMMUNOLOGY, 2019, 39 : S45 - S46
  • [29] Lentiviral Gene Therapy of Chronic Granulomatous Disease: Functional Assessment of Universal and Tissue-Specific Promoters
    Yuan, Haokun
    Wu, Xiaomei
    Liu, Hongwei
    Chang, Lung-Ji
    HUMAN GENE THERAPY, 2023, 34 (1-2) : 19 - 29
  • [30] Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatous Disease
    Capo, Valentina
    Farinelli, Giada
    Chiriaco, Maria
    Zonari, Erika
    Scaramuzza, Samantha
    Di Matteo, Gigliola
    Sergi, Lucia Sergi
    Migliavacca, Maddalena
    Hernandez, Raisa Jofra
    Kajaste-Rudnitski, Anna
    Trono, Didier
    Grez, Manuel
    Rossi, Paolo
    Finocchi, Andrea
    Naldini, Luigi
    Gentner, Bernhard
    Aiuti, Alessandro
    MOLECULAR THERAPY, 2014, 22 : S261 - S261
12345