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- [22] DISRUPTION OF THE ADENOSINE-DEAMINASE (ADA) GENE USING A DICISTRONIC PROMOTERLESS CONSTRUCT - PRODUCTION OF AN ADA-DEFICIENT HOMOZYGOTE ES CELL-LINETRANSGENIC RESEARCH, 1995, 4 (04) : 247 - 255VAULONT, S论文数: 0 引用数: 0 h-index: 0机构: UNIV CAMBRIDGE,CANC RES CAMPAIGN,INST CANC & DEV BIOL,WELLCOME,CAMBRIDGE CB2 1QR,ENGLANDDAINES, S论文数: 0 引用数: 0 h-index: 0机构: UNIV CAMBRIDGE,CANC RES CAMPAIGN,INST CANC & DEV BIOL,WELLCOME,CAMBRIDGE CB2 1QR,ENGLANDEVANS, M论文数: 0 引用数: 0 h-index: 0机构: UNIV CAMBRIDGE,CANC RES CAMPAIGN,INST CANC & DEV BIOL,WELLCOME,CAMBRIDGE CB2 1QR,ENGLAND
- [23] Outcomes following treatment for ADA-deficient severe combined immunodeficiency: a report from the PIDTCBLOOD, 2022, 140 (07) : 685 - 705Cuvelier, Geoffrey D. E.论文数: 0 引用数: 0 h-index: 0机构: Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, Canada Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaLogan, Brent R.论文数: 0 引用数: 0 h-index: 0机构: Med Coll Wisconsin, Div Biostat, Milwaukee, WI 53226 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaProckop, Susan E.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Stem Cell Transplant Serv, Dana Farber Canc Inst, Boston, MA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaBuckley, Rebecca H.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ Med Ctr, Durham, NC USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaKuo, Caroline Y.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, David Geffen Sch Med, Dept Pediat, Div Allergy Immunol Rheumatol, Los Angeles, CA 90095 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaGriffith, Linda M.论文数: 0 引用数: 0 h-index: 0机构: NIAID, Div Allergy Immunol & Transplantat, NIA, NIH, 9000 Rockville Pike, Bethesda, MD 20892 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaLiu, Xuerong论文数: 0 引用数: 0 h-index: 0机构: Med Coll Wisconsin, Div Biostat, Milwaukee, WI 53226 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaYip, Alison论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Benioff Childrens Hosp, San Francisco, CA 94143 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaHershfield, Michael S.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ Med Ctr, Durham, NC USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaAyoub, Paul G.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaMoore, Theodore B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Mattel Childrens Hosp, Dept Pediat Hematol Oncol, Los Angeles, CA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaDorsey, Morna J.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Benioff Childrens Hosp, San Francisco, CA 94143 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaO'Reilly, Richard J.论文数: 0 引用数: 0 h-index: 0机构: Mem Sloan Kettering Canc Ctr, MSK Kids, Stem Cell Transplantat & Cellular Therapy, 1275 York Ave, New York, NY 10021 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaKapoor, Neena论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp, Div Hematol Oncol & Blood & Marrow Transplant, Los Angeles, CA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaPai, Sung-Yun论文数: 0 引用数: 0 h-index: 0机构: NCI, Immune Deficiency Cellular Therapy Program, Ctr Canc Res, Bethesda, MD 20892 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaKapadia, Malika论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dana Farber Canc Inst, Boston, MA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaEbens, Christen L.论文数: 0 引用数: 0 h-index: 0机构: MHlth Fairview Masonic Childrens Hosp, Div Pediat Blood & Marrow Transplant & Cellular T, Minneapolis, MN USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaSatter, Lisa R. Forbes论文数: 0 引用数: 0 h-index: 0机构: Texas Childrens Hosp, Baylor Coll Med, Immunol Allergy & Retrovirol, Houston, TX 77030 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaBurroughs, Lauri M.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Dept Pediat, Fred Hutchinson Canc Res Ctr, Seattle, WA 98195 USA Seattle Childrens Hosp, Seattle, WA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaPetrovic, Aleksandra论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Dept Pediat, Fred Hutchinson Canc Res Ctr, Seattle, WA 98195 USA Seattle Childrens Hosp, Seattle, WA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaChellapandian, Deepak论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins All Childrens Hosp, Ctr Cell & Gene Therapy Nonmalignant Condit, St Petersburg, FL USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaHeimall, Jennifer论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Childrens Hosp Philadelphia, Perelman Sch Med, Dept Pediat,Div Allergy & Immunol, Philadelphia, PA 19104 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaShyr, David C.论文数: 0 引用数: 0 h-index: 0机构: Lucile Packard Childrens Hosp, Stanford Sch Med, Div Hematol Oncol Stem Cell Transplantat & Regene, Palo Alto, CA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaRayes, Ahmad论文数: 0 引用数: 0 h-index: 0机构: Univ Utah, Primary Childrens Hosp, Salt Lake City, UT USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaBednarski, Jeffrey J.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, St Louis Childrens Hosp, St Louis, MO 63110 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, Canada论文数: 引用数: h-index:机构:Chandrakasan, Shanmuganathan论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Atlanta, Bone Marrow Transplantat & Immune Deficiency, Atlanta, GA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaGillio, Alfred P.论文数: 0 引用数: 0 h-index: 0机构: Hackensack Univ Med Ctr, Childrens Canc Inst, Hackensack, NJ USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaMadden, Lisa论文数: 0 引用数: 0 h-index: 0机构: Methodist Childrens Hosp South Texas, San Antonio, TX USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaQuigg, Troy C.论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Pediat Blood & Marrow Transplant & Cellular Thera, Helen DeVos Childrens Hosp, Coll Human Med, Grand Rapids, MI USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaCaywood, Emi H.论文数: 0 引用数: 0 h-index: 0机构: Thomas Jefferson Univ, Nemours Childrens Hlth, Wilmington, DE USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaSaldana, Blachy J. Davila论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl Hosp, Div Blood & Marrow Transplantat, Washington, DC USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaDeSantes, Kenneth论文数: 0 引用数: 0 h-index: 0机构: Univ Wisconsin, Amer Family Childrens Hosp, Div Pediat Hematol Oncol & Bone Marrow Transplant, Madison, WI USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaEissa, Hesham论文数: 0 引用数: 0 h-index: 0机构: Div Pediat Hematol Oncol BMT, Aurora, CO USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaGoldman, Frederick D.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Div Pediat Hematol & Oncol & Bone Marrow Transpla, Birmingham, AL USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaRozmus, Jacob论文数: 0 引用数: 0 h-index: 0机构: British Columbia Childrens Hosp, Vancouver, BC, Canada Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaShah, Ami J.论文数: 0 引用数: 0 h-index: 0机构: Lucile Packard Childrens Hosp, Stanford Sch Med, Div Hematol Oncol Stem Cell Transplantat & Regene, Palo Alto, CA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaVander Lugt, Mark T.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Blood & Marrow Transplant Program, Ann Arbor, MI 48109 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaThakar, Monica S.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Dept Pediat, Fred Hutchinson Canc Res Ctr, Seattle, WA 98195 USA Seattle Childrens Hosp, Seattle, WA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaParrott, Roberta E.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ Med Ctr, Durham, NC USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaMartinez, Caridad论文数: 0 引用数: 0 h-index: 0机构: Texas Childrens Hosp, Baylor Coll Med, Hematol Oncol BMT, Houston, TX USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaLeiding, Jennifer W.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Div Allergy & Immunol, St Petersburg, FL USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaTorgerson, Troy R.论文数: 0 引用数: 0 h-index: 0机构: Allen Inst Immunol, Seattle, WA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaPulsipher, Michael A.论文数: 0 引用数: 0 h-index: 0机构: Univ Utah, Div Pediat Hematol & Oncol, Intermt Primary Childrens Hosp, Huntsman Canc Inst,Spencer Fox Eccles Sch Med, Salt Lake City, UT USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaNotarangelo, Luigi D.论文数: 0 引用数: 0 h-index: 0机构: NIAID, Lab Clin Immunol & Microbiol, NIH, 9000 Rockville Pike, Bethesda, MD 20892 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaCowan, Morton J.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Benioff Childrens Hosp, San Francisco, CA 94143 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaDvorak, Christopher C.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Benioff Childrens Hosp, San Francisco, CA 94143 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaHaddad, Elie论文数: 0 引用数: 0 h-index: 0机构: Univ Montreal, Dept Pediat, Ctr Hosp Univ CHU St Justine, Montreal, PQ, Canada Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaPuck, Jennifer M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Benioff Childrens Hosp, San Francisco, CA 94143 USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, CanadaKohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Manitoba, CancerCare Manitoba, Manitoba Blood & Marrow Transplant Program, Winnipeg, MB, Canada
- [24] ADA-deficient severe combined immunodeficiency presenting with disseminated varicella infection after vaccinationANNALS OF ALLERGY ASTHMA & IMMUNOLOGY, 2008, 100 (01) : A19 - A19Lebak, N. M.论文数: 0 引用数: 0 h-index: 0Zhao, W.论文数: 0 引用数: 0 h-index: 0Irani, A. M.论文数: 0 引用数: 0 h-index: 0
- [25] Effects of Vector Backbone and Pseudotype on Lentiviral Vector-mediated Gene Transfer: Studies in Infant ADA-Deficient Mice and Rhesus MonkeysMOLECULAR THERAPY, 2014, 22 (10) : 1803 - 1816Sarracino, Denise Carbonaro论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USATaranta, Alice F.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Ctr Fetal Monkey Gene Transfer Heart Lung & Blood, Davis, CA 95616 USA Univ Calif Davis, Dept Pediat, Davis, CA 95616 USA Univ Calif Davis, Dept Cell Biol & Human Anat, Davis, CA 95616 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USALee, C. Chang I.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Ctr Fetal Monkey Gene Transfer Heart Lung & Blood, Davis, CA 95616 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USAMartinez, Michele论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Ctr Fetal Monkey Gene Transfer Heart Lung & Blood, Davis, CA 95616 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USALin, Xiangyang论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USAWang, Xiaoyan论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Gen Internal Med & Hlth Serv Res, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USAHardee, Cinnamon L.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USAGeiger, Sabine论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USAKahl, Christoph A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Div Res lmmunol BMT, Los Angeles, CA 90027 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USAKohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Dept Pediat, Los Angeles, CA 90095 USA Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA 90095 USA
- [26] Alterations in the adenosine metabolism and CD39/CD73 adenosinergic machinery cause loss of Treg cell function and autoimmunity in ADA-deficient SCIDBLOOD, 2012, 119 (06) : 1428 - 1439Sauer, Aisha V.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyBrigida, Immacolata论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy Univ Roma Tor Vergata, Dept Publ Hlth & Cell Biol, Rome, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyCarriglio, Nicola论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy Univ Roma Tor Vergata, Dept Publ Hlth & Cell Biol, Rome, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyHernandez, Raisa Jofra论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyScaramuzza, Samantha论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyClavenna, Daniela论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Dept Oncol, Pathol Unit, I-20132 Milan, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalySanvito, Francesca论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Dept Oncol, Pathol Unit, I-20132 Milan, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyPoliani, Pietro L.论文数: 0 引用数: 0 h-index: 0机构: Univ Brescia, Dept Pathol, Brescia, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyGagliani, Nicola论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyCarlucci, Filippo论文数: 0 引用数: 0 h-index: 0机构: Univ Siena, Dept Internal Med Endocrine Metab Sci & Biochem, I-53100 Siena, Italy Azienda Osped Univ Senese, Unita Operat Complessa Clin Pathol, Siena, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyTabucchi, Antonella论文数: 0 引用数: 0 h-index: 0机构: Univ Siena, Dept Internal Med Endocrine Metab Sci & Biochem, I-53100 Siena, Italy Azienda Osped Univ Senese, Unita Operat Complessa Clin Pathol, Siena, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyRoncarolo, Maria Grazia论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyTraggiai, Elisabetta论文数: 0 引用数: 0 h-index: 0机构: Inst G Gaslini, Ist Ricovero & Cura Carattere Sci, Div Pediat 2, Genoa, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyVilla, Anna论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy CNR, Ist Ric Genet & Biomed, I-20133 Milan, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, ItalyAiuti, Alessandro论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy Univ Roma Tor Vergata, Dept Publ Hlth & Cell Biol, Rome, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy
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- [29] Dosing and Re-Administration of Intravenous Lentiviral Vector for Liver-Directed Gene Transfer in Young Rhesus Monkeys and ADA-Deficient MiceMOLECULAR THERAPY, 2016, 24 : S302 - S303Carbonaro-Sarracino, Denise A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USATarantal, Alice F.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Dept Pediat, Davis, CA USA Univ Calif Davis, Dept Cell Biol & Human Anat, Davis, CA USA Univ Calif Davis, Calif Natl Primate Res Ctr, Davis, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USALee, Chang I.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Dept Pediat, Davis, CA USA Univ Calif Davis, Dept Cell Biol & Human Anat, Davis, CA USA Univ Calif Davis, Calif Natl Primate Res Ctr, Davis, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAKaufman, Michael L.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAMartinez, Michele论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Dept Pediat, Davis, CA USA Univ Calif Davis, Dept Cell Biol & Human Anat, Davis, CA USA Univ Calif Davis, Calif Natl Primate Res Ctr, Davis, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAClark, Danielle N.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAKoziol, Colin论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAKohn, Donald B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Microbiol Immunol & Mol Genet & Pediat, Los Angeles, CA USA Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA
- [30] SUPPRESSION OF AN ANTIBODY TO ADENOSINE-DEAMINASE (ADA) IN AN ADA-DEFICIENT PATIENT RECEIVING POLYETHYLENE-GLYCOL MODIFIED ADENOSINE-DEAMINASEANNALS OF ALLERGY, 1993, 70 (06): : 462 - 466CHUN, JD论文数: 0 引用数: 0 h-index: 0机构: DUKE UNIV, SCH MED, DEPT MED, DURHAM, NC 27706 USALEE, N论文数: 0 引用数: 0 h-index: 0机构: DUKE UNIV, SCH MED, DEPT MED, DURHAM, NC 27706 USAKOBAYASHI, RH论文数: 0 引用数: 0 h-index: 0机构: DUKE UNIV, SCH MED, DEPT MED, DURHAM, NC 27706 USACHAFFEE, S论文数: 0 引用数: 0 h-index: 0机构: DUKE UNIV, SCH MED, DEPT MED, DURHAM, NC 27706 USAHERSHFIELD, MS论文数: 0 引用数: 0 h-index: 0机构: DUKE UNIV, SCH MED, DEPT MED, DURHAM, NC 27706 USASTIEHM, ER论文数: 0 引用数: 0 h-index: 0机构: DUKE UNIV, SCH MED, DEPT MED, DURHAM, NC 27706 USA