Enabling redosing of AAV by immune management in Pompe disease: Preclinical to clinical studies

被引：1
|
作者：
Corti, Manuela [1 ]
Cleaver, Brian [1 ]
Clement, Nathalie [1 ]
Wang, Genscheng [2 ]
Benson, Janet [2 ]
Tarantal, Alice [3 ]
Herzog, Roland [1 ]
Byrne, Barry [1 ]
机构：
[1] Univ Florida, Gainesville, FL USA
[2] LRRI, Lovelance, NM USA
[3] Univ Calif Davis, Davis, CA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2018年 / 123卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2017.12.067
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
58
引用
收藏
页码：S34 / S34
页数：1
相关论文
共 50 条
  • [21] Endothelin in Nondiabetic Chronic Kidney Disease: Preclinical and Clinical Studies
    Culshaw, Geoff J.
    MacIntyre, Iain M.
    Dhaun, Neeraj
    Webb, David J.
    SEMINARS IN NEPHROLOGY, 2015, 35 (02) : 176 - 187
  • [22] CHANGING THE CLINICAL COURSE OF INFANTILE POMPE DISEASE WITH IMMUNE MODULATION STRATEGIES: 12 YEARS OF EXPERIENCE
    Desai, Ankit
    Kazi, Zoheb
    Bali, Deeksha
    Rehder, Catherine
    Rosenberg, Amy
    Kishnani, Priya
    MOLECULAR GENETICS AND METABOLISM, 2019, 127 (03) : 243 - 243
  • [23] CHANGING THE CLINICAL COURSE OF INFANTILE POMPE DISEASE WITH IMMUNE MODULATION STRATEGIES: 12 YEARS OF EXPERIENCE
    Desai, Ankit
    Kazi, Zoheb
    Bali, Deeksha
    Rehder, Catherine
    Rosenberg, Amy
    Kishnani, Priya
    MOLECULAR GENETICS AND METABOLISM, 2019, 126 (03) : 280 - 280
  • [24] Long term outcome and clinical experience on immune tolerance induction therapies in infantile Pompe disease
    Stephanie Austin
    Priya Kishnani
    BMC Musculoskeletal Disorders, 14 (Suppl 2)
  • [25] Changing the clinical course of infantile Pompe disease with immune modulation strategies: 12 years of experience
    Desai, Ankit K.
    Kazi, Zoheb B.
    Bali, Deeksha S.
    Rehder, Catherine W.
    Richards, Susan
    Rosenberg, Amy S.
    Kishnani, Priya S.
    MOLECULAR GENETICS AND METABOLISM, 2019, 126 (02) : S48 - S48
  • [26] Long Term Outcome and Clinical Experience on Immune Tolerance Induction Therapies in Infantile Pompe Disease
    Banugaria, Suhrad
    Prater, Sean
    Bali, Deeksha
    Rehder, Catherine
    Rosenberg, Amy
    Kishnani, Priya
    MOLECULAR GENETICS AND METABOLISM, 2012, 105 (02) : S20 - S20
  • [27] The Impact of Metformin on Tumor-Infiltrated Immune Cells: Preclinical and Clinical Studies
    Abdelmoneim, Mohamed
    Aboalela, Mona Alhussein
    Naoe, Yoshinori
    Matsumura, Shigeru
    Eissa, Ibrahim Ragab
    Bustos-Villalobos, Itzel
    Sibal, Patricia Angela
    Takido, Yuhei
    Kodera, Yasuhiro
    Kasuya, Hideki
    INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2023, 24 (17)
  • [28] Physiotherapy management in late-onset Pompe disease: Clinical practice in 88 patients
    Favejee, Marein M.
    Huisstede, Bionka M. A.
    Bussmann, Johannes B. J.
    Kruijshaar, Michelle E.
    van der Ploeg, Ans T.
    MOLECULAR GENETICS AND METABOLISM, 2012, 107 (1-2) : 111 - 115
  • [29] Role of Flavonoids in Management of Various Biological Targets in Alzheimer's Disease: Evidence from Preclinical to Clinical Studies
    Alharbi, Khalid Saad
    Shaikh, Mohammad Arshad Javed
    Imam, Syed Sarim
    Alshehri, Sultan
    Ghoneim, Mohammed M.
    Almalki, Waleed Hassan
    Singh, Sachin Kumar
    Kumar, Deepak
    Kumar, Avvaru Praveen
    Dua, Kamal
    Chellappan, Dinesh Kumar
    Paudel, Keshav Raj
    Gupta, Gaurav
    CURRENT MEDICINAL CHEMISTRY, 2023, 30 (18) : 2061 - 2074
  • [30] Therapeutic potential of flavonoids in the management of obesity-induced Alzheimer's disease: an overview of preclinical and clinical studies
    Kothawade, Sakshi M.
    Buttar, Harpal Singh
    Tuli, Hardeep Singh
    Kaur, Ginpreet
    NAUNYN-SCHMIEDEBERGS ARCHIVES OF PHARMACOLOGY, 2023, 396 (11) : 2813 - 2830
12345