Enabling redosing of AAV by immune management in Pompe disease: Preclinical to clinical studies

被引：1
|
作者：
Corti, Manuela [1 ]
Cleaver, Brian [1 ]
Clement, Nathalie [1 ]
Wang, Genscheng [2 ]
Benson, Janet [2 ]
Tarantal, Alice [3 ]
Herzog, Roland [1 ]
Byrne, Barry [1 ]
机构：
[1] Univ Florida, Gainesville, FL USA
[2] LRRI, Lovelance, NM USA
[3] Univ Calif Davis, Davis, CA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2018年 / 123卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2017.12.067
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
58
引用
收藏
页码：S34 / S34
页数：1
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