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- [31] Study on the efficacy, safety, and biomarkers of nusinersen in type II and III spinal muscular atrophy in childrenFRONTIERS IN PEDIATRICS, 2023, 11Chen, Liyuan论文数: 0 引用数: 0 h-index: 0机构: Guangdong Med Univ, Dept Neurol, Dongguan Childrens Hosp, Dongguan, Peoples R China Guangdong Med Univ, Dept Neurol, Dongguan Childrens Hosp, Dongguan, Peoples R ChinaLiu, Fen论文数: 0 引用数: 0 h-index: 0机构: Guangdong Med Univ, Dept Neurol, Dongguan Childrens Hosp, Dongguan, Peoples R China Guangdong Med Univ, Dept Neurol, Dongguan Childrens Hosp, Dongguan, Peoples R ChinaFang, Danna论文数: 0 引用数: 0 h-index: 0机构: Guangdong Med Univ, Dept Neurol, Dongguan Childrens Hosp, Dongguan, Peoples R China Guangdong Med Univ, Dept Neurol, Dongguan Childrens Hosp, Dongguan, Peoples R ChinaLi, Jianwei论文数: 0 引用数: 0 h-index: 0机构: Guangdong Med Univ, Dept Neurol, Dongguan Childrens Hosp, Dongguan, Peoples R China Guangdong Med Univ, Dept Neurol, Dongguan Childrens Hosp, Dongguan, Peoples R China
- [32] Ultrasound assisted lumbar intrathecal administration of nusinersen in adult patients with spinal muscular atrophy: A case seriesMUSCLE & NERVE, 2021, 64 (05) : 594 - 599Zanfini, Bruno Antonio论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, ItalyCatarci, Stefano论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, ItalyPatanella, Agata Katia论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ A Gemelli IRCCS, Ctr Clin Nemo, Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, ItalyPane, Marika论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ A Gemelli IRCCS, Ctr Clin Nemo Pediat, Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, ItalyFrassanito, Luciano论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, ItalyFilipponi, Eleonora论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, ItalyMercuri, Eugenio论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ A Gemelli IRCCS, Ctr Clin Nemo Pediat, Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, ItalySabatelli, Mario论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ A Gemelli IRCCS, Ctr Clin Nemo, Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, ItalyDraisci, Gaetano论文数: 0 引用数: 0 h-index: 0机构: Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, Italy Fdn Policlin Univ Agostino Gemelli IRCCS, Dept Emergency Anesthesiol & Reanimat Sci, Largo A Gemelli 8, I-00168 Rome, Italy
- [33] Children with spinal muscular atrophy treated with nusinersen/risdiplamRESPIROLOGY, 2023, 28 : 204 - 205Chacko, A.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Brisbane, Qld, Australia Univ Queensland, Child Hlth Res Ctr, Brisbane, Qld, Australia Queensland Childrens Hosp, Brisbane, Qld, AustraliaSly, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Queensland, Child Hlth Res Ctr, Brisbane, Qld, Australia Queensland Childrens Hosp, Brisbane, Qld, AustraliaDeegan, S.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Brisbane, Qld, Australia Queensland Childrens Hosp, Brisbane, Qld, AustraliaYoung, E.论文数: 0 引用数: 0 h-index: 0机构: Griffith Univ, Menzies Hlth Inst Queensland, Brisbane, Qld, Australia Queensland Childrens Hosp, Brisbane, Qld, AustraliaGauld, L.论文数: 0 引用数: 0 h-index: 0机构: Queensland Childrens Hosp, Brisbane, Qld, Australia Univ Queensland, Child Hlth Res Ctr, Brisbane, Qld, Australia Queensland Childrens Hosp, Brisbane, Qld, Australia
- [34] Muscle impairment in MRI affect variability in treatment response to nusinersen in patients with spinal muscular atrophy type 2 and 3: A retrospective cohort studyBRAIN & DEVELOPMENT, 2023, 45 (03): : 161 - 170Shimizu-Motohashi, Yuko论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, JapanChiba, Emiko论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Radiol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan论文数: 引用数: h-index:机构:Yajima, Hiroyuki论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Neurol & Psychiat, Translat Med Ctr, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, JapanIshiyama, Akihiko论文数: 0 引用数: 0 h-index: 0机构: Tokyo Metropolitan Neurol Hosp, Dept Neuropediat, 2-6-1 Musashidai, Fuchu, Tokyo 1830042, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, JapanTakeshita, Eri论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, JapanSato, Noriko论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Radiol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, JapanOba, Mari论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Neurol & Psychiat, Translat Med Ctr, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Clin Res & Educ Promot Div, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, JapanSasaki, Masayuki论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, JapanIto, Shuichi论文数: 0 引用数: 0 h-index: 0机构: Yokohama City Univ, Grad Sch Med, Dept Pediat, 3-9 Fukuura,Kanazawa Ku, Yokohama, Kanagawa 2360004, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, JapanKomaki, Hirofumi论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Neurol & Psychiat, Translat Med Ctr, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Clin Res & Educ Promot Div, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan Natl Ctr Neurol & Psychiat, Natl Ctr Hosp, Dept Child Neurol, 4-1-1 Ogawahigashi Cho, Kodaira, Tokyo 1878551, Japan
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