Identification of drugs to treat MPS I caused by nonsense mutations

被引：0
|
作者：
Bedwell, David [1 ]
Gunn, Gwen [1 ]
Siddiqui, Amna [1 ]
Du, Ming [1 ]
Bostwick, Bob [2 ]
Suto, Mark [2 ]
Row, Steven [1 ]
Keeling, Kim M. [1 ]
机构：
[1] Univ Alabama Birmingham, Birmingham, AL USA
[2] Southern Res, Birmingham, AL USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2017年 / 120卷 / 1-2期
关键词：
D O I：
10.1016/j.ymgme.2016.11.035
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
26
引用
收藏
页码：S25 / S25
页数：1
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