Correction of Hunter Syndrome in the MPSII Mouse Model by AAV2/8-Mediated Gene Delivery

被引：0
|
作者：
Cardone, Monica
Polito, Vinicia Assunta
Pepe, Stefano
Mann, Linda
D'Azzo, Alessandra
Auricchio, Alberto
Ballabio, Andrea
Cosma, Maria Pia
机构：
[1] TIGEM Telethon Inst Genet & Med, Naples, Italy
[2] St Jude Childrens Res Hosp, Memphis, TN 38105 USA
来源：
MOLECULAR THERAPY | 2006年 / 13卷
关键词：
D O I：
10.1016/j.ymthe.2006.08.234
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
209
引用
收藏
页码：S81 / S81
页数：1
相关论文
共 50 条
  • [31] AAV2/5-mediated NGF gene delivery protects septal cholinergic neurons following axotomy
    Wu, K
    Meyer, EM
    Bennett, JA
    Meyers, CA
    Hughes, JA
    King, MA
    BRAIN RESEARCH, 2005, 1061 (02) : 107 - 113
  • [32] Gene delivery to breast cancer by incorporated EpCAM targeted DARPins into AAV2
    Ya-feng Lv
    Hao Zhang
    Zhi Cui
    Cui-jiao Ma
    Yu-ling Li
    Hua Lu
    Hong-yan Wu
    Jian-lin Yang
    Chun-yu Cao
    Wen-zheng Sun
    Xiao-fei Huang
    BMC Cancer, 23
  • [33] Improved method of recombinant AAV2 delivery for systemic targeted gene therapy
    Mah, C
    Fraites, TJ
    Zolotukhin, I
    Song, SH
    Flotte, TR
    Dobson, J
    Batich, C
    Byrne, BJ
    MOLECULAR THERAPY, 2002, 6 (01) : 106 - 112
  • [34] Intravitreal AAV2 gene delivery to feline retinal ganglion cells (RGCs)
    Oikawa, Kazuya
    Kiland, Julie
    Eaton, Seth
    Torne, Odalys
    Mathu, Virginia
    Nickells, Robert
    McLellan, Gillian
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2023, 64 (08)
  • [35] Phenotypic correction of a mouse model of hemophilia A using AAV2 vectors encoding the heavy and light chains of FVIII
    Scallan, CD
    Liu, TY
    Parker, AE
    Patarroyo-White, SL
    Chen, HF
    Jiang, HY
    Vargas, J
    Nagy, D
    Powell, SK
    Wright, JF
    Sarkar, R
    Kazazian, HH
    McClelland, A
    Couto, LB
    BLOOD, 2003, 102 (12) : 3919 - 3926
  • [36] A Penetrable AAV2 Capsid Variant for Efficient Intravitreal Gene Delivery to the Retina
    He, Xiaoyu
    Fu, Yidian
    Xu, Yangfan
    Ma, Liang
    Chai, Peiwei
    Shi, Hanhan
    Yao, Yizheng
    Ge, Shengfang
    Jia, Renbing
    Wen, Xuyang
    Yang, Zhi
    Fan, Xianqun
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2025, 66 (01)
  • [37] The utility of AAV2/rh10 for gene delivery to murine photoreceptors
    Palfi, Arpad
    Chadderton, Naomi
    Millington-Ward, Sophia
    O'Reilly, Mary
    Bennett, Jean
    Kenna, Paul
    Farrar, Jane
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2014, 55 (13)
  • [38] E-Selectin/AAV2/2 Gene Therapy Alters Angiogenesis and Inflammatory Gene Profiles in Mouse Gangrene Model
    Ribieras, Antoine J.
    Ortiz, Yulexi Y.
    Li, Yan
    Huerta, Carlos T.
    Le, Nga
    Shao, Hongwei
    Vazquez-Padron, Roberto I.
    Liu, Zhao-Jun
    Velazquez, Omaida C.
    FRONTIERS IN CARDIOVASCULAR MEDICINE, 2022, 9
  • [39] Gene Therapy using an AAV2/8 vector corrects the biochemical imbalances in a murine model of MNGIE
    Torres-Torronteras, J.
    Viscomi, C.
    Cabrera, R.
    Camara, Y.
    Barquinero, J.
    Di Meo, I.
    Hirano, M.
    Zeviani, M.
    Marti, R.
    HUMAN GENE THERAPY, 2013, 24 (12) : A54 - A55
  • [40] Development of Adeno-Associated Virus (AAV9)-Mediated Gene Delivery to Treat a Mouse Model of Cockayne Syndrome
    Hatano, Silveli Suzuki
    Sriramvenugopal, Mughil
    Witko, Rachael
    Palwai, Poojan
    Rizzo, Skylar
    Vermeij, Wilbert P.
    Hoeijmakers, Jan H. J.
    Brooks, P. J.
    Kang, Peter B.
    Pacak, Christina A.
    MOLECULAR THERAPY, 2019, 27 (04) : 116 - 116
12345