共 50 条
- [21] Drug development of vamorolone for Duchenne muscular dystrophyNEUROMUSCULAR DISORDERS, 2017, 27 : S217 - S218论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Morgenroth, L.论文数: 0 引用数: 0 h-index: 0机构: TRiNDS, Pittsburgh, PA USA Univ Pittsburgh, Pittsburgh, PA USADamsker, J.论文数: 0 引用数: 0 h-index: 0机构: ReveraGen BioPharma, Silver Spring, MD USA Univ Pittsburgh, Pittsburgh, PA USASmith, A.论文数: 0 引用数: 0 h-index: 0机构: TRiNDS, Pittsburgh, PA USA Univ Pittsburgh, Pittsburgh, PA USAHathout, Y.论文数: 0 引用数: 0 h-index: 0机构: Binghamton Univ, Binghamton, NY USA Univ Pittsburgh, Pittsburgh, PA USACnaan, A.论文数: 0 引用数: 0 h-index: 0机构: TRiNDS, Philadelphia, PA USA Univ Pittsburgh, Pittsburgh, PA USA论文数: 引用数: h-index:机构:Mah, J.论文数: 0 引用数: 0 h-index: 0机构: Alberta Childrens Prov Gen Hosp, Calgary, AB, Canada Univ Pittsburgh, Pittsburgh, PA USAByrne, B.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Pittsburgh, Pittsburgh, PA USACastro, D.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA Univ Pittsburgh, Pittsburgh, PA USAFinkel, R.论文数: 0 引用数: 0 h-index: 0机构: Nemours Childrens Hosp, Orlando, FL USA Univ Pittsburgh, Pittsburgh, PA USAKuntz, N.论文数: 0 引用数: 0 h-index: 0机构: Lurie Childrens Hosp, Chicago, IL USA Univ Pittsburgh, Pittsburgh, PA USAMcDonald, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Sacramento, CA 95817 USA Univ Pittsburgh, Pittsburgh, PA USANevo, Y.论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Tel Aviv, Israel Univ Pittsburgh, Pittsburgh, PA USARyan, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Melbourne, Melbourne, Vic, Australia Univ Pittsburgh, Pittsburgh, PA USATulinius, M.论文数: 0 引用数: 0 h-index: 0机构: Gothenburg Univ, Gothenburg, Sweden Univ Pittsburgh, Pittsburgh, PA USAWebster, R.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Westmead, Westmead, NSW, Australia Univ Pittsburgh, Pittsburgh, PA USAHoffman, E.论文数: 0 引用数: 0 h-index: 0机构: ReveraGen BioPharma, Silver Spring, MD USA Univ Pittsburgh, Pittsburgh, PA USA
- [22] Development of PPMO for the Treatment of Duchenne Muscular DystrophyNEUROLOGY, 2018, 90Passini, Marco A.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USAGan, Li论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USAWood, Jenna A.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USAYao, Monica论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USAEstrella, Nelsa L.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USATreleaven, Chris M.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USAWentworth, Bruce M.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USACharleston, Jay S.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USARutkowski, Joseph V.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USAHanson, Gunnar J.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut, Cambridge, MA USA Sarepta Therapeut, Cambridge, MA USA
- [23] Drug development progress in duchenne muscular dystrophyFRONTIERS IN PHARMACOLOGY, 2022, 13Deng, Jiexin论文数: 0 引用数: 0 h-index: 0机构: Henan Univ, Sch Nursing & Hlth, Kaifeng, Peoples R China Henan Univ, Sch Nursing & Hlth, Kaifeng, Peoples R ChinaZhang, Junshi论文数: 0 引用数: 0 h-index: 0机构: Henan Univ, Huaihe Hosp, Dept Neurol, Kaifeng, Peoples R China Henan Univ, Sch Nursing & Hlth, Kaifeng, Peoples R ChinaShi, Keli论文数: 0 引用数: 0 h-index: 0机构: Henan Univ, Sch Med, Kaifeng, Peoples R China Henan Univ, Sch Nursing & Hlth, Kaifeng, Peoples R ChinaLiu, Zhigang论文数: 0 引用数: 0 h-index: 0机构: Henan Univ, Affiliated Hosp 1, Dept Orthoped, Kaifeng, Peoples R China Henan Univ, Sch Nursing & Hlth, Kaifeng, Peoples R China
- [24] STANDING BALANCE IN HEALTHY BOYS AND IN CHILDREN WITH DUCHENNE MUSCULAR-DYSTROPHYARCHIVES OF PHYSICAL MEDICINE AND REHABILITATION, 1981, 62 (07): : 324 - 327KELLY, CR论文数: 0 引用数: 0 h-index: 0机构: UNIV KANSAS,DEPT REHABIL MED,KANSAS CITY,KS 66103REDFORD, JB论文数: 0 引用数: 0 h-index: 0机构: UNIV KANSAS,DEPT REHABIL MED,KANSAS CITY,KS 66103ZILBER, S论文数: 0 引用数: 0 h-index: 0机构: UNIV KANSAS,DEPT REHABIL MED,KANSAS CITY,KS 66103MADDEN, PA论文数: 0 引用数: 0 h-index: 0机构: UNIV KANSAS,DEPT REHABIL MED,KANSAS CITY,KS 66103
- [25] RELIABILITY OF GONIOMETRIC MEASUREMENTS IN PATIENTS WITH DUCHENNE MUSCULAR-DYSTROPHYPHYSICAL THERAPY, 1985, 65 (09): : 1339 - 1342PANDYA, S论文数: 0 引用数: 0 h-index: 0机构: VANDERBILT UNIV, MED CTR, MUSCULAR DYSTROPHY CLIN, NASHVILLE, TN 37212 USAFLORENCE, JM论文数: 0 引用数: 0 h-index: 0机构: VANDERBILT UNIV, MED CTR, MUSCULAR DYSTROPHY CLIN, NASHVILLE, TN 37212 USAKING, WM论文数: 0 引用数: 0 h-index: 0机构: VANDERBILT UNIV, MED CTR, MUSCULAR DYSTROPHY CLIN, NASHVILLE, TN 37212 USAROBISON, JD论文数: 0 引用数: 0 h-index: 0机构: VANDERBILT UNIV, MED CTR, MUSCULAR DYSTROPHY CLIN, NASHVILLE, TN 37212 USAOXMAN, M论文数: 0 引用数: 0 h-index: 0机构: VANDERBILT UNIV, MED CTR, MUSCULAR DYSTROPHY CLIN, NASHVILLE, TN 37212 USAPROVINCE, MA论文数: 0 引用数: 0 h-index: 0机构: VANDERBILT UNIV, MED CTR, MUSCULAR DYSTROPHY CLIN, NASHVILLE, TN 37212 USA
- [26] Reliability of the Performance of Upper Limb assessment in Duchenne muscular dystrophyNEUROMUSCULAR DISORDERS, 2014, 24 (03) : 201 - 206Pane, Marika论文数: 0 引用数: 0 h-index: 0机构: Child Neurol & Psychiat Unit, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalyMazzone, Elena S.论文数: 0 引用数: 0 h-index: 0机构: Child Neurol & Psychiat Unit, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalyFanelli, Lavinia论文数: 0 引用数: 0 h-index: 0机构: Child Neurol & Psychiat Unit, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalyDe Sanctis, Roberto论文数: 0 引用数: 0 h-index: 0机构: Child Neurol & Psychiat Unit, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalyBianco, Flaviana论文数: 0 引用数: 0 h-index: 0机构: Child Neurol & Psychiat Unit, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalySivo, Serena论文数: 0 引用数: 0 h-index: 0机构: Child Neurol & Psychiat Unit, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalyD'Amico, Adele论文数: 0 引用数: 0 h-index: 0机构: Bambino Gesu Pediat Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Dis, Rome, Italy Child Neurol & Psychiat Unit, Rome, Italy论文数: 引用数: h-index:机构:Battini, Roberta论文数: 0 引用数: 0 h-index: 0机构: Stella Maris Inst, Dept Dev Neurosci, Pisa, Italy Child Neurol & Psychiat Unit, Rome, ItalyScutifero, Marianna论文数: 0 引用数: 0 h-index: 0机构: Univ Naples Federico II, Dept Expt Med, I-80138 Naples, Italy Child Neurol & Psychiat Unit, Rome, ItalyPetillo, Roberta论文数: 0 引用数: 0 h-index: 0机构: Univ Naples Federico II, Dept Expt Med, I-80138 Naples, Italy Child Neurol & Psychiat Unit, Rome, ItalyFrosini, Silvia论文数: 0 引用数: 0 h-index: 0机构: Stella Maris Inst, Dept Dev Neurosci, Pisa, Italy Child Neurol & Psychiat Unit, Rome, ItalyScalise, Roberta论文数: 0 引用数: 0 h-index: 0机构: Child Neurol & Psychiat Unit, Rome, Italy Child Neurol & Psychiat Unit, Rome, Italy论文数: 引用数: h-index:机构:Bruno, Claudio论文数: 0 引用数: 0 h-index: 0机构: G Gaslini Inst Children, Neuromuscular Dis Unit, Genoa, Italy Child Neurol & Psychiat Unit, Rome, ItalyPedemonte, Marina论文数: 0 引用数: 0 h-index: 0机构: G Gaslini Inst Children, Neuromuscular Dis Unit, Genoa, Italy Child Neurol & Psychiat Unit, Rome, ItalyMongini, Tiziana论文数: 0 引用数: 0 h-index: 0机构: Univ Turin, Neuromuscular Ctr, SG Battista Hosp, I-10124 Turin, Italy Child Neurol & Psychiat Unit, Rome, ItalyPegoraro, Elena论文数: 0 引用数: 0 h-index: 0机构: Univ Padua, Dept Neurosci, I-35100 Padua, Italy Child Neurol & Psychiat Unit, Rome, ItalyBrustia, Francesca论文数: 0 引用数: 0 h-index: 0机构: IRCCS C Mondino Fdn, Pavia, Italy Child Neurol & Psychiat Unit, Rome, ItalyGardani, Alice论文数: 0 引用数: 0 h-index: 0机构: IRCCS C Mondino Fdn, Pavia, Italy Child Neurol & Psychiat Unit, Rome, ItalyBerardinelli, Angela论文数: 0 引用数: 0 h-index: 0机构: IRCCS C Mondino Fdn, Pavia, Italy Child Neurol & Psychiat Unit, Rome, ItalyLanzillotta, Valentina论文数: 0 引用数: 0 h-index: 0机构: Univ Turin, Neuromuscular Ctr, SG Battista Hosp, I-10124 Turin, Italy Child Neurol & Psychiat Unit, Rome, Italy论文数: 引用数: h-index:机构:Cavallaro, Filippo论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, Dept Neurosci Psychiat & Anaesthesiol, I-98100 Messina, Italy Child Neurol & Psychiat Unit, Rome, ItalySframeli, Maria论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, Dept Neurosci Psychiat & Anaesthesiol, I-98100 Messina, Italy Child Neurol & Psychiat Unit, Rome, ItalyBello, Luca论文数: 0 引用数: 0 h-index: 0机构: IRCCS Eugenio Medea, Bosisio Parini, Italy Child Neurol & Psychiat Unit, Rome, ItalyBarp, Andrea论文数: 0 引用数: 0 h-index: 0机构: IRCCS Eugenio Medea, Bosisio Parini, Italy Child Neurol & Psychiat Unit, Rome, ItalyBonfiglio, Serena论文数: 0 引用数: 0 h-index: 0机构: Bellaria Hosp, Child Neurol & Psychiat Unit, IRCCS Inst Neurol Sci, Bologna, Italy Child Neurol & Psychiat Unit, Rome, ItalyRolle, Enrica论文数: 0 引用数: 0 h-index: 0机构: Ctr Clin Nemo, Milan, Italy Child Neurol & Psychiat Unit, Rome, ItalyColia, Giulia论文数: 0 引用数: 0 h-index: 0机构: Bambino Gesu Pediat Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Dis, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalyCatteruccia, Michela论文数: 0 引用数: 0 h-index: 0机构: Bambino Gesu Pediat Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Dis, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalyPalermo, Concetta论文数: 0 引用数: 0 h-index: 0机构: Child Neurol & Psychiat Unit, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalyD'Angelo, Grazia论文数: 0 引用数: 0 h-index: 0机构: IRCCS Eugenio Medea, Bosisio Parini, Italy Child Neurol & Psychiat Unit, Rome, ItalyPini, Antonella论文数: 0 引用数: 0 h-index: 0机构: Bellaria Hosp, Child Neurol & Psychiat Unit, IRCCS Inst Neurol Sci, Bologna, Italy Child Neurol & Psychiat Unit, Rome, ItalyIotti, Elena论文数: 0 引用数: 0 h-index: 0机构: Neurol Inst C Besta, Pediat Neurol Unit, Milan, Italy Neurol Inst C Besta, Neuroradiol Unit, Milan, Italy Child Neurol & Psychiat Unit, Rome, ItalyGorni, Ksenija论文数: 0 引用数: 0 h-index: 0机构: Ctr Clin Nemo, Milan, Italy Child Neurol & Psychiat Unit, Rome, ItalyBaranello, Giovanni论文数: 0 引用数: 0 h-index: 0机构: Neurol Inst C Besta, Pediat Neurol Unit, Milan, Italy Neurol Inst C Besta, Neuroradiol Unit, Milan, Italy Child Neurol & Psychiat Unit, Rome, ItalyMorandi, Lucia论文数: 0 引用数: 0 h-index: 0机构: Neurol Inst C Besta, Pediat Neurol Unit, Milan, Italy Neurol Inst C Besta, Neuroradiol Unit, Milan, Italy Child Neurol & Psychiat Unit, Rome, ItalyBertini, Enrico论文数: 0 引用数: 0 h-index: 0机构: Bambino Gesu Pediat Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Dis, Rome, Italy Child Neurol & Psychiat Unit, Rome, ItalyPolitano, Luisa论文数: 0 引用数: 0 h-index: 0机构: Univ Naples Federico II, Dept Expt Med, I-80138 Naples, Italy Child Neurol & Psychiat Unit, Rome, ItalySormani, MariaPia论文数: 0 引用数: 0 h-index: 0机构: Univ Genoa, Dept Hlth Sci, Biostat Unit, I-16126 Genoa, Italy Child Neurol & Psychiat Unit, Rome, ItalyMercuri, Eugenio论文数: 0 引用数: 0 h-index: 0机构: Child Neurol & Psychiat Unit, Rome, Italy Child Neurol & Psychiat Unit, Rome, Italy
- [27] Longitudinal reliability of outcome measures in patients with Duchenne muscular dystrophyMUSCLE & NERVE, 2020, 61 (01) : 63 - 68Nagy, Sara论文数: 0 引用数: 0 h-index: 0机构: Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland Univ Basel, Univ Hosp Basel, Dept Neurol, Basel, Switzerland Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, SwitzerlandSchadelin, Sabine论文数: 0 引用数: 0 h-index: 0机构: Univ Basel, Clin Trial Unit, Basel, Switzerland Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, SwitzerlandHafner, Patricia论文数: 0 引用数: 0 h-index: 0机构: Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, SwitzerlandBonati, Ulrike论文数: 0 引用数: 0 h-index: 0机构: Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland Univ Basel, Univ Hosp Basel, Dept Neurol, Basel, Switzerland Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, SwitzerlandScherrer, Delia论文数: 0 引用数: 0 h-index: 0机构: Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland论文数: 引用数: h-index:机构:Schmidt, Simone论文数: 0 引用数: 0 h-index: 0机构: Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, SwitzerlandOrsini, Anna-Lena论文数: 0 引用数: 0 h-index: 0机构: Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland Univ Basel, Univ Hosp Basel, Dept Neurol, Basel, Switzerland Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland论文数: 引用数: h-index:机构:Fischer, Dirk论文数: 0 引用数: 0 h-index: 0机构: Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland Univ Basel, Childrens Hosp, Div Neuropaediat, Spitalstr 33, CH-4031 Basel, Switzerland
- [28] RELIABILITY OF TESTING MEASURES IN DUCHENNE OR BECKER MUSCULAR-DYSTROPHYARCHIVES OF PHYSICAL MEDICINE AND REHABILITATION, 1991, 72 (05): : 315 - 319BARR, AE论文数: 0 引用数: 0 h-index: 0机构: HOSP SPECIAL SURG,DEPT REHABIL SERV,NEW YORK,NY 10021DIAMOND, BE论文数: 0 引用数: 0 h-index: 0机构: HOSP SPECIAL SURG,DEPT REHABIL SERV,NEW YORK,NY 10021WADE, CK论文数: 0 引用数: 0 h-index: 0机构: HOSP SPECIAL SURG,DEPT REHABIL SERV,NEW YORK,NY 10021HARASHIMA, T论文数: 0 引用数: 0 h-index: 0机构: HOSP SPECIAL SURG,DEPT REHABIL SERV,NEW YORK,NY 10021PECORELLA, WA论文数: 0 引用数: 0 h-index: 0机构: HOSP SPECIAL SURG,DEPT REHABIL SERV,NEW YORK,NY 10021POTTS, CC论文数: 0 引用数: 0 h-index: 0机构: HOSP SPECIAL SURG,DEPT REHABIL SERV,NEW YORK,NY 10021ROSENTHAL, H论文数: 0 引用数: 0 h-index: 0机构: HOSP SPECIAL SURG,DEPT REHABIL SERV,NEW YORK,NY 10021FLEISS, JL论文数: 0 引用数: 0 h-index: 0机构: HOSP SPECIAL SURG,DEPT REHABIL SERV,NEW YORK,NY 10021MCMAHON, DJ论文数: 0 引用数: 0 h-index: 0机构: HOSP SPECIAL SURG,DEPT REHABIL SERV,NEW YORK,NY 10021
- [29] RELIABILITY OF GONIOMETRIC MEASUREMENTS IN PATIENTS WITH DUCHENNE MUSCULAR-DYSTROPHYPHYSICAL THERAPY, 1984, 64 (05): : 732 - 732PANDYA, S论文数: 0 引用数: 0 h-index: 0机构: UNIV ROCHESTER,SCH MED & DENT,DEPT NEUROL,ROCHESTER,NY 14642FLORENCE, J论文数: 0 引用数: 0 h-index: 0机构: UNIV ROCHESTER,SCH MED & DENT,DEPT NEUROL,ROCHESTER,NY 14642KING, W论文数: 0 引用数: 0 h-index: 0机构: UNIV ROCHESTER,SCH MED & DENT,DEPT NEUROL,ROCHESTER,NY 14642ROBISON, J论文数: 0 引用数: 0 h-index: 0机构: UNIV ROCHESTER,SCH MED & DENT,DEPT NEUROL,ROCHESTER,NY 14642SIGNORE, L论文数: 0 引用数: 0 h-index: 0机构: UNIV ROCHESTER,SCH MED & DENT,DEPT NEUROL,ROCHESTER,NY 14642
- [30] Evaluation of narrative abilities in patients suffering from Duchenne Muscular DystrophyBRAIN AND LANGUAGE, 2007, 102 (01) : 1 - 12Marini, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Udine, Cattedra Psicol Linguaggio, I-33100 Udine, ItalyLorusso, M. L.论文数: 0 引用数: 0 h-index: 0机构: Univ Udine, Cattedra Psicol Linguaggio, I-33100 Udine, ItalyD'Angelo, M. G.论文数: 0 引用数: 0 h-index: 0机构: Univ Udine, Cattedra Psicol Linguaggio, I-33100 Udine, ItalyCivati, F.论文数: 0 引用数: 0 h-index: 0机构: Univ Udine, Cattedra Psicol Linguaggio, I-33100 Udine, ItalyTurconi, A. C.论文数: 0 引用数: 0 h-index: 0机构: Univ Udine, Cattedra Psicol Linguaggio, I-33100 Udine, ItalyFabbro, F.论文数: 0 引用数: 0 h-index: 0机构: Univ Udine, Cattedra Psicol Linguaggio, I-33100 Udine, ItalyBresolin, N.论文数: 0 引用数: 0 h-index: 0机构: Univ Udine, Cattedra Psicol Linguaggio, I-33100 Udine, Italy