Preclinical Development of AAV Vectors for the Treatment of X-linked Retinitis Pigmentosa Caused by RPGR Mutations

被引：0
|
作者：
Wu, Zhijian [1 ]
Hiriyanna, Suja [1 ]
Qian, Haohua [1 ]
Mookherjee, Suddhasil [1 ]
Kaneshiro, Kayleigh [1 ]
Campos, Maria M. [1 ]
Fariss, Robert N. [1 ]
Li, Tiansen [1 ]
Swaroop, Anand [1 ]
Colosi, Peter [1 ]
机构：
[1] NEI, NIH, Bethesda, MD 20892 USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2014年 / 55卷 / 13期
关键词：
538 gene transfer/gene therapy; 688; retina; 648; photoreceptors;
D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
3305
引用
收藏
页数：3
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