共 50 条
- [31] Gene therapy offers new hope for children with metachromatic leukodystrophy LANCET, 2022, 399 (10322): : 338 - 339
- [33] AAV gene therapy vectors in the TMJ CLINICAL AND EXPERIMENTAL DENTAL RESEARCH, 2022, 8 (06): : 1561 - 1566
- [35] In vivo gene therapy of metachromatic leukodystrophy by lentiviral vectors: correction of neuropathology and protection against learning impairments in affected mice Nature Medicine, 2001, 7 : 310 - 316
- [37] Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits mice JOURNAL OF CLINICAL INVESTIGATION, 2006, 116 (11): : 3070 - 3082