Transposon-Based, Targeted Ex Vivo Gene Therapy to Treat Age-Related Macular Degeneration (TargetAMD)

被引:1
|
作者
Thumann, Gabriele [1 ]
Perdikomati-Dahmen, Maria [2 ]
Izsvak, Zsuzsanna [3 ]
Ivics, Zoltan [4 ]
Garcia Layana, Alfredo [5 ]
Ronchetti, Mattia [6 ]
Petrovski, Goran
Scherman, Daniel [7 ]
Aranda, Pablo [8 ]
Pouillot, Severine [9 ]
Binder, Susanne [10 ]
Johnen, Sandra [11 ]
Van den Berg, Joost [12 ]
机构
[1] Univ Geneva, CH-1211 Geneva 4, Switzerland
[2] Rhein Westfal TH Aachen, Aachen, Germany
[3] Max Delbruck Ctr Mol Med, Berlin, Germany
[4] Paul Ehrlich Inst, Frankfurt, Germany
[5] Univ Navarra, E-31080 Pamplona, Spain
[6] IGEA SPA, Rome, Italy
[7] CNRS, F-75700 Paris, France
[8] 3P Biopharmaceut SL, Madrid, Spain
[9] GenoSafe SAS, Evry, France
[10] Rudolf Fdn Hosp, Vienna, Austria
[11] Univ Klinikum Aachen, Aachen, Germany
[12] Stichting Amsterdam Biotherapeut Unit, Amsterdam, Netherlands
关键词
SLEEPING-BEAUTY TRANSPOSON; ANTIBIOTIC-RESISTANCE MARKERS; PIGMENT EPITHELIAL-CELLS; PLASMIDS FREE; EXPRESSION; PFARS;
D O I
10.1089/humc.2015.2519
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
[No abstract available]
引用
收藏
页码:97 / 100
页数:4
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