Intrapleural Administration of a Second-Generation Oxidation Resistant Alpha 1-Antitrypsin Gene Therapy for Alpha 1-Antitrypsin Deficiency

被引:0
|
作者
Stiles, K. M. [1 ]
Sosulski, M. L. [1 ]
De, B. P. [1 ]
Driscoll, S. R. [1 ]
Kaminsky, S. M. [1 ]
Crystal, R. G. [1 ]
机构
[1] Weill Cornell Med Coll, New York, NY USA
关键词
D O I
暂无
中图分类号
R4 [临床医学];
学科分类号
1002 ; 100602 ;
摘要
A2284
引用
收藏
页数:1
相关论文
共 50 条
  • [41] Augmentation Therapy for α1-Antitrypsin Deficiency
    Georges S. Juvelekian
    James K. Stoller
    Drugs, 2004, 64 : 1743 - 1756
  • [42] The bronchopulmonary pathology of alpha 1-antitrypsin (AAT) deficiency: Findings of the death review Committee of the National Registry for Individuals with Severe Deficiency of Alpha 1-antitrypsin
    Tomashefski, JF
    Crystal, RG
    Wiedemann, HP
    Mascha, E
    MODERN PATHOLOGY, 2003, 16 (01) : 315A - 315A
  • [43] Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency
    Rosenberg, Jonathan B.
    De Bishnu, P.
    Greco, Alessandria
    Gorman, Nicholas
    Kooner, Vikrum
    Chen, Alvin
    Yost-Bido, Melissa
    Munoz-Zuluaga, Carlos
    Kaminsky, Stephen M.
    Rostami, Mahboubeh
    Monette, Sebastien
    Crystal, Ronald G.
    Sondhi, Dolan
    HUMAN GENE THERAPY, 2023, 34 (3-4) : 139 - 149
  • [44] Self-Administration of Augmentation Therapy for Alpha 1-Antitrypsin Deficiency in Italy: a survey study
    Vianello, Andrea
    Lococo, Sara
    Corda, Luciano
    Torrazza, Mario
    Baderna, Paolo
    Bargagli, Elena
    Zamparelli, Stefano Sanduzzi
    De Marchi, Leonardo Bertagna
    Molena, Beatrice
    Lionello, Federico
    Achille, Alessia
    Guarnieri, Gabriella
    EUROPEAN RESPIRATORY JOURNAL, 2024, 64
  • [45] Emphysema in nonsmokers: Alpha 1-antitrypsin deficiency and other causes
    Lee, P
    Gildea, TR
    Stoller, JK
    CLEVELAND CLINIC JOURNAL OF MEDICINE, 2002, 69 (12) : 928 - +
  • [46] LIQUEFYING PANNICULITIS - CUTANEOUS SYMPTOMS OF ALPHA 1-ANTITRYPSIN DEFICIENCY
    GROSSHAN.E
    WARTER, J
    STORCK, D
    BASSET, A
    BULLETIN DE LA SOCIETE FRANCAISE DE DERMATOLOGIE ET DE SYPHILIGRAPHIE, 1973, 80 (03): : 244 - 247
  • [47] Alpha 1-antitrypsin deficiency and the risk for Wegener's granulomatosis
    Mahr, Alfred
    Edberg, Jeffrey
    Stone, John
    Hoffman, Gary
    St Clair, E. William
    Specks, Ulrich
    Dellaripa, Paul
    Spiera, Robert
    Rouhani, Farshid
    Brantly, Mark
    Merkel, Peter
    APMIS, 2009, 117 : 157 - 157
  • [49] Cirrhosis in children and SZ phenotype alpha 1-antitrypsin deficiency
    Budin, C
    Rivet, C
    Dumortier, J
    Legall, C
    Bouvier, R
    Lachaux, A
    GASTROENTEROLOGIE CLINIQUE ET BIOLOGIQUE, 2005, 29 (02): : 206 - 207
  • [50] Acquired alpha 1-antitrypsin deficiency in tropical pulmonary eosinophilia
    Ray, Debidas
    Harikrishna, S.
    Immanuel, Chandra
    Victor, Lalitha
    Subramanyam, Sudha
    Kumaraswami, V.
    INDIAN JOURNAL OF MEDICAL RESEARCH, 2011, 134 (01) : 79 - 82